日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

First-in-human high dose AAV9 intrathecal gene therapy for paediatric CLN7 disease: a phase 1, open-label, single ascending dose, non-randomised clinical trial

首次人体高剂量AAV9鞘内基因疗法治疗儿童CLN7疾病:一项1期、开放标签、单次递增剂量、非随机临床试验

Greenberg, Benjamin M; Minassian, Berge; Messahel, Souad; Edgar, Veronica Bordes; Lowden, Andrea; Dahshi, Hamza; Nettesheim, Emily R; Nguyen, Hoang H; Hughes, Samuel; Muthukumar, Alagar R; Srinivasan, Kalayarasan; Iannaccone, Susan; Varadarajan, Ganapathy; Gray, Steven J; Kayani, Saima N

Low Intensity Focused Ultrasound Neuromodulation in Psychiatric Disorders: Mechanisms, Models, and Missing Links

低强度聚焦超声神经调控在精神疾病中的应用:机制、模型和缺失环节

Arulpragasam, Amanda R; Theyel, Brian; Barredo, Jennifer; Pouille, Frederic; Gillotti, Julia G; Greenberg, Benjamin D; Wout-Frank, Mascha van 't; Philip, Noah S

Clinical and radiological outcomes of directed treatment transitions from Gilenya(®) to generic fingolimod

从吉列尼亚® (Gilenya®) 过渡到通用芬戈莫德的定向治疗方案的临床和放射学结果

Patel, Mahi A; Punnen, Tom G; Shan, Kevin S; McCreary, Morgan C; Wright, Crystal M; Munoz, Shanan B; Hardeman, Paula; Burgess, Katy W; Greenberg, Benjamin M; Horton, Lindsay A; Sguigna, Peter V; Tardo, Lauren M; Stüve, Olaf; Okuda, Darin T

CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

CNM-Au8 在肌萎缩侧索硬化症中的应用:HEALEY ALS 平台试验

Berry, James D; Maragakis, Nicholas J; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Stommel, Elijah W; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin J; Simmons, Zachary; Miller, Timothy; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo Jr; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney E; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Rynders, Austin; Evan, Jacob; Evan, Jeremy; Hartford, Alan; Sepassi, Marjan; Ho, Karen S; Glanzman, Robert; Greenberg, Benjamin; Hotchkin, Michael T; Paganoni, Sabrina; Cudkowicz, Merit E

Genome-wide analyses identify 30 loci associated with obsessive-compulsive disorder

全基因组分析确定了30个与强迫症相关的基因位点

Strom, Nora I; Gerring, Zachary F; Galimberti, Marco; Yu, Dongmei; Halvorsen, Matthew W; Abdellaoui, Abdel; Rodriguez-Fontenla, Cristina; Sealock, Julia M; Bigdeli, Tim; Coleman, Jonathan R; Mahjani, Behrang; Thorp, Jackson G; Bey, Katharina; Burton, Christie L; Luykx, Jurjen J; Zai, Gwyneth; Alemany, Silvia; Andre, Christine; Askland, Kathleen D; Bäckman, Julia; Banaj, Nerisa; Barlassina, Cristina; Nissen, Judith Becker; Bienvenu, O Joseph; Black, Donald; Bloch, Michael H; Børte, Sigrid; Bosch, Rosa; Breen, Michael; Brennan, Brian P; Brentani, Helena; Buxbaum, Joseph D; Bybjerg-Grauholm, Jonas; Byrne, Enda M; Cabana-Dominguez, Judit; Camarena, Beatriz; Camarena, Adrian; Cappi, Carolina; Carracedo, Angel; Casas, Miguel; Cavallini, Maria Cristina; Ciullo, Valentina; Cook, Edwin H; Crosby, Jesse; Cullen, Bernadette A; De Schipper, Elles J; Delorme, Richard; Djurovic, Srdjan; Elias, Jason A; Estivill, Xavier; Falkenstein, Martha J; Fundin, Bengt T; Garner, Lauryn; Gironda, Christina; Goes, Fernando S; Grados, Marco A; Grove, Jakob; Guo, Wei; Haavik, Jan; Hagen, Kristen; Harrington, Kelly; Havdahl, Alexandra; Höffler, Kira D; Hounie, Ana G; Hucks, Donald; Hultman, Christina; Janecka, Magdalena; Jenike, Eric; Karlsson, Elinor K; Kelley, Kara; Klawohn, Julia; Krasnow, Janice E; Krebs, Kristi; Lange, Christoph; Lanzagorta, Nuria; Levey, Daniel; Lindblad-Toh, Kerstin; Macciardi, Fabio; Maher, Brion; Mathes, Brittany; McArthur, Evonne; McGregor, Nathaniel; McLaughlin, Nicole C; Meier, Sandra; Miguel, Euripedes C; Mulhern, Maureen; Nestadt, Paul S; Nurmi, Erika L; O'Connell, Kevin S; Osiecki, Lisa; Ousdal, Olga Therese; Palviainen, Teemu; Pedersen, Nancy L; Piras, Fabrizio; Piras, Federica; Potluri, Sriramya; Rabionet, Raquel; Ramirez, Alfredo; Rauch, Scott; Reichenberg, Abraham; Riddle, Mark A; Ripke, Stephan; Rosário, Maria C; Sampaio, Aline S; Schiele, Miriam A; Skogholt, Anne Heidi; Sloofman, Laura G; Smit, Jan; Artigas, María Soler; Thomas, Laurent F; Tifft, Eric; Vallada, Homero; van Kirk, Nathanial; Veenstra-VanderWeele, Jeremy; Vulink, Nienke N; Walker, Christopher P; Wang, Ying; Wendland, Jens R; Winsvold, Bendik S; Yao, Yin; Zhou, Hang; Agrawal, Arpana; Alonso, Pino; Berberich, Götz; Bucholz, Kathleen K; Bulik, Cynthia M; Cath, Danielle; Denys, Damiaan; Eapen, Valsamma; Edenberg, Howard; Falkai, Peter; Fernandez, Thomas V; Fyer, Abby J; Gaziano, J M; Geller, Dan A; Grabe, Hans J; Greenberg, Benjamin D; Hanna, Gregory L; Hickie, Ian B; Hougaard, David M; Kathmann, Norbert; Kennedy, James; Lai, Dongbing; Landén, Mikael; Hellard, Stéphanie Le; Leboyer, Marion; Lochner, Christine; McCracken, James T; Medland, Sarah E; Mortensen, Preben B; Neale, Benjamin M; Nicolini, Humberto; Nordentoft, Merete; Pato, Michele; Pato, Carlos; Pauls, David L; Piacentini, John; Pittenger, Christopher; Posthuma, Danielle; Ramos-Quiroga, Josep Antoni; Rasmussen, Steven A; Richter, Margaret A; Rosenberg, David R; Ruhrmann, Stephan; Samuels, Jack F; Sandin, Sven; Sandor, Paul; Spalletta, Gianfranco; Stein, Dan J; Stewart, S Evelyn; Storch, Eric A; Stranger, Barbara E; Turiel, Maurizio; Werge, Thomas; Andreassen, Ole A; Børglum, Anders D; Walitza, Susanne; Hveem, Kristian; Hansen, Bjarne K; Rück, Christian; Martin, Nicholas G; Milani, Lili; Mors, Ole; Reichborn-Kjennerud, Ted; Ribasés, Marta; Kvale, Gerd; Mataix-Cols, David; Domschke, Katharina; Grünblatt, Edna; Wagner, Michael; Zwart, John-Anker; Breen, Gerome; Nestadt, Gerald; Kaprio, Jaakko; Arnold, Paul D; Grice, Dorothy E; Knowles, James A; Ask, Helga; Verweij, Karin J; Davis, Lea K; Smit, Dirk J; Crowley, James J; Scharf, Jeremiah M; Stein, Murray B; Gelernter, Joel; Mathews, Carol A; Derks, Eske M; Mattheisen, Manuel

Pathway to response: Associations between individual electrical fields and psychophysiological habituation to predict clinical outcomes to transcranial direct current stimulation combined with virtual reality for PTSD

反应路径:个体电场与心理生理习惯化之间的关联,用于预测经颅直流电刺激联合虚拟现实治疗创伤后应激障碍的临床疗效

van 't Wout-Frank, Mascha; Sorensen, David O; Parra, Lucas C; Huang, Yu; Harle, Alexis; Greenberg, Benjamin D; Arulpragasam, Amanda R; Philip, Noah S

Long-Term Efficacy and Safety of Satralizumab in Patients With Neuromyelitis Optica Spectrum Disorder From the SAkuraMoon Open-Label Extension Study

来自 SAkuraMoon 开放标签扩展研究的 Satralizumab 治疗视神经脊髓炎谱系障碍患者的长期疗效和安全性

Bennett, Jeffrey L; Fujihara, Kazuo; Saiz, Albert; Traboulsee, Anthony L; Greenberg, Benjamin M; Weinshenker, Brian G; Patti, Francesco; Kleiter, Ingo; Palace, Jacqueline; De Seze, Jerome; Evans, Rachael; Blondeau, Kathleen; Klingelschmitt, Gaëlle; Vodopivec, Ivana; Rahim, Masouda; Yamamura, Takashi

The Evolution of Anti-CD20 Treatment for Multiple Sclerosis: Optimization of Antibody Characteristics and Function

多发性硬化症抗CD20治疗的演变:抗体特性和功能的优化

Cree, Bruce A C; Berger, Joseph R; Greenberg, Benjamin

Correction: The Evolution of Anti‑CD20 Treatment for Multiple Sclerosis: Optimization of Antibody Characteristics and Function

更正:抗CD20治疗多发性硬化症的演变:抗体特性和功能的优化

Cree, Bruce A C; Berger, Joseph R; Greenberg, Benjamin

Weight Loss in Veterans with Schizophrenia and Multimorbidity Prescribed Semaglutide: Results From a National Retrospective Cohort Study

接受司美格鲁肽治疗的精神分裂症合并多种疾病退伍军人的体重减轻:一项全国回顾性队列研究的结果

Browne, Julia; Wu, Wen-Chih; Jiang, Lan; Bayer, Thomas A; Kunicki, Zachary J; Thompson, Matthew; Bozzay, Melanie L; De Vito, Alyssa N; Howe, Matthew D; Singh, Mriganka; Primack, Jennifer M; McGeary, John E; Maharaj, Ritesh; Kelso, Catherine M; Philip, Noah S; Greenberg, Benjamin D; Rudolph, James L