Exploiting the diphtheria toxin internalization receptor enhances delivery of proteins to lysosomes for enzyme replacement therapy
利用白喉毒素内化受体增强蛋白质向溶酶体的输送,用于酶替代疗法
期刊:Science Advances
影响因子:11.7
doi:10.1126/sciadv.abb0385
Seiji N Sugiman-Marangos, Greg L Beilhartz, Xiaochu Zhao, Dongxia Zhou, Rong Hua, Peter K Kim, James M Rini, Berge A Minassian, Roman A Melnyk