日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Enhancing the potency of in vivo lentiviral vector mediated gene therapy to hepatocytes.

增强体内慢病毒载体介导的基因治疗对肝细胞的效力

Canepari Cesare, Milani Michela, Simoni Chiara, Starinieri Francesco, Volpin Monica, Fabiano Anna, Biffi Mauro, Russo Fabio, Norata Rossana, Rocchi Martina, Brombin Chiara, Cugnata Federica, Montini Eugenio, Sanvito Francesca, Grompe Markus, Cantore Alessio

Hepatocyte senescence and persistent liver injury in Fanconi anemia

范可尼贫血症中的肝细胞衰老和持续性肝损伤

Koo, Jane; Snyder, Alana J; Campbell, Kathleen; Miller, Erica; O'Conner, Allison; Grompe, Markus; Mehta, Parinda A; Myers, Kasiani C; Davies, Stella M

Cell networks in the mouse liver during partial hepatectomy.

小鼠部分肝切除术期间肝脏内的细胞网络。

Li Bin, Rodrigo-Torres Daniel, Pelz Carl, Innes Brendan, Canaday Pamela, Chai Sunghee, Zandstra Peter, Bader Gary D, Grompe Markus

One Shock, Not One Cure: Electroporation Reveals Disease-Specific Constraints in Hepatocyte Gene Editing Therapy.

一次电击,而非一次治愈:电穿孔揭示肝细胞基因编辑疗法中疾病特异性限制

Clark Callie, Pokhrel Menam, Arthur Benjamin, Suresh Pramita, Ates Ilayda, Gibson Justin, Dhungana Abishek, Mehlem Ryan, Boysia Andrew, Padalkar Mugdha V, Pokhrel Achala, Echesabal-Chen Jing, Vonada Anne, Stamatikos Alexis, Savinova Olga V, Grompe Markus, Cottle Renee N

A porcine model of Fanconi anemia

范可尼贫血症的猪模型

Hergert, Brandon; Whitworth, Kristin M; Goldman, Devorah C; Moreau, Lisa; McQueen, Kelsey; Parmar, Kalindi; D'Andrea, Alan; Samuel, Melissa S; Wells, Kevin D; Prather, Randall S; Dorell, Craig; Grompe, Markus; Fleming, William H

Impact of a Preclinical Elective on Medical Student Attitudes Toward People With Substance Use Disorders

临床前选修课对医学生对待物质使用障碍者的态度的影响

Cooper, Colleen; Rdesinski, Rebecca E; Douglas, Angela; Grompe, Heidi; Kamsky, Hannah; Cantone, Rebecca E

Complete correction of murine phenylketonuria by selection-enhanced hepatocyte transplantation

通过选择性增强肝细胞移植完全纠正小鼠苯丙酮尿症

Vonada, Anne; Wakefield, Leslie; Martinez, Michael; Harding, Cary O; Grompe, Markus; Tiyaboonchai, Amita

AAV Capsid Screening for Translational Pig Research Using a Mouse Xenograft Liver Model

利用小鼠异种移植肝模型进行AAV衣壳筛选以用于转化猪研究

Willimann, Melanie; Tiyaboonchai, Amita; Adachi, Kei; Li, Bin; Waldburger, Lea; Nakai, Hiroyuki; Grompe, Markus; Thöny, Beat

Rapid in vivo multiplexed editing (RIME) of the adult mouse liver

成年小鼠肝脏的快速体内多重编辑(RIME)

Takeshi Katsuda,Hector Cure,Jonathan Sussman,Kamen P Simeonov,Christopher Krapp,Zoltan Arany,Markus Grompe,Ben Z Stanger

Strong ubiquitous micro-promoters for recombinant adeno-associated viral vectors

用于重组腺相关病毒载体的强效普遍存在的微启动子

Chai, Sunghee; Wakefield, Leslie; Norgard, Mason; Li, Bin; Enicks, David; Marks, Daniel L; Grompe, Markus