日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Directed evolution-based discovery of ligands for in vivo restimulation of chimeric antigen receptor T cells

基于定向进化的嵌合抗原受体T细胞体内再刺激配体的发现

Grzywa, Tomasz M; Neeser, Alexandra; Ramasubramanian, Ranjani; Romanov, Anna; Tannir, Ryan; Mehta, Naveen K; Cossette, Benjamin; Morgan, Duncan M; Goncalves, Beatriz; Sukaj, Ina; Bergaggio, Elisa; Kadauke, Stephan; Myers, Regina M; Paruzzo, Luca; Ghilardi, Guido; Cozzone, Austin; Schuster, Stephen J; Frey, Noelle; Zhang, Libin; Yousefpour, Parisa; Abraham, Wuhbet; Suh, Heikyung; Ruella, Marco; Grupp, Stephan A; Chiarle, Roberto; Wittrup, K Dane; Ma, Leyuan; Irvine, Darrell J

Preinfusion risk factors for the development of severe neurotoxicity following CART therapy in pediatric patients

儿童患者接受 CAR-T 疗法后发生严重神经毒性的输注前风险因素

Diorio, Caroline; Myers, Regina M; Li, Yimei; Liu, Hongyan; Belfer, Samuel; DiNofia, Amanda; Leahy, Allison Barz; Newman, Haley; Dolan, Jillian; Martinez, Zachary; Elhachimi, Amira; Lindell, Robert B; Mullen, Cassidy; Li, Alexander; Kim, John; Teachey, David T; Maude, Shannon L; Grupp, Stephan A; McGuire, Jennifer L

CCR4 expression defines a targetable subset of T-cell acute lymphoblastic leukemia

CCR4表达定义了T细胞急性淋巴细胞白血病的一个可靶向亚群。

Xu, Jason; McCoy, Michael; Martinez, Zachary; Sussman, Jonathan H; Gao, Daniel; Vincent, Tiffaney; Wang, Hunter; Ma, Connie; Elghawy, Omar; Chen, Gregory M; Yang, Austin G; Pölönen, Petri; Natan, Keanu; Shraim, Rawan; Newman, Haley; Hofmann, Ted J; Scoma, Samantha; DiNofia, Amanda M; Hunger, Stephen P; Yang, Jun J; Mullighan, Charles G; Bernt, Kathrin M; Hexner, Elizabeth O; Grupp, Stephan A; Watanabe, Keisuke; June, Carl H; Tan, Kai; Teachey, David T; Diorio, Caroline

[Chinese diagnosis and treatment guideline for pediatric acute promyelocytic leukemia(2025)]

【中国儿童急性早幼粒细胞白血病诊疗指南(2025)】

Silbert, Sara K; Rankin, Alexander W; Hoang, Chloe N; Semchenkova, Alexandra; Myers, Regina M; Zerkalenkova, Elena; Wang, Hao-Wei; Kovach, Alexandra E; Yuan, Constance M; Delgado Colon, Dana; Vasseur, Loïc; Bataller, Alex; John, Samuel; Utley Lyons, Kaylyn; Friedes, Barbara; Alonso-Saladrigues, Anna; Abdel-Azim, Hisham; Balducci, Estelle; Aljudi, Ahmed Assim; Balsat, Marie; Biery, D Nathan; Chamdin, Aghiad; Chang, Bill H; Cuevo, Raymund S; De Moerloose, Barbara; Dickens, David S; Duffner, Ulrich; Duployez, Nicolas; El Chaer, Firas; Elliott, Michelle Ann; Escherich, Gabriele; Fernandes, Sneha; Fitzjohn, Mandi R; Gahvari, Zhubin; Grupp, Stephan A; He, Rui Rochelle; Harrison, Cynthia; Hergott, Christopher B; Hsieh, Emily M; Kim, Annette S; Kuo, Dennis J; Larson, Daniel P; Lee, Benjamin J; Leguay, Thibaut; Lindsley, R Coleman; Mangaonkar, Abhishek A; Mezger, Kerstin; Pacenta, Holly L; Pan, Jing; Provost, Marlie; Puri, Latika; Raikar, Sunil S; Martinez, Armando; Bristol, Isabella; Murphy, Kyle; Reiman, Lauren; Redell, Michele; Reed, Kelly; Roth-Guepin, Gabrielle; Rubinstein, Jeremy; Savaşan, Süreyya; Schafernak, Kristian; Stevens, Alexandra; Talleur, Aimee; Torres Carapia, Naomi; Vargaftig, Jacques; Vatsayan, Anant; Wölfl, Matthias; Zhao, Liping; Rives, Susana; Fabrizio, Vanessa A; Sasaki, Koji; Aldoss, Ibrahim; Boissel, Nicolas; Rheingold, Susan R; Davis, Kara L; Ghorashian, Sara; Jacoby, Elad; Popov, Alexander; Lamble, Adam J; Shah, Nirali N

IKAROS levels are associated with antigen escape in CD19- and CD22-targeted therapies for B-cell malignancies

IKAROS 水平与 CD19 和 CD22 靶向治疗 B 细胞恶性肿瘤中的抗原逃逸相关。

Domizi, Pablo; Sarno, Jolanda; Jager, Astraea; Merchant, Milton; Pacheco, Kaithlen Zen B; Yamada-Hunter, Sean A; Rotiroti, Maria Caterina; Liu, Yuxuan; Baskar, Reema; Reynolds, Warren D; Sworder, Brian J; Sahaf, Bita; Bendall, Sean C; Mullighan, Charles G; Alizadeh, Ash A; Leahy, Allison B; Myers, Regina M; Yates, Bonnie; Wang, Hao-Wei; Shah, Nirali N; Majzner, Robbie G; Mackall, Crystal L; Grupp, Stephan A; Barrett, David M; Sotillo, Elena; Davis, Kara L

CD22-targeted chimeric antigen receptor-modified T cells for children and adults with relapse of B-cell acute lymphoblastic leukemia after CD19-directed immunotherapy

CD22靶向嵌合抗原受体修饰的T细胞用于治疗CD19靶向免疫疗法后复发的B细胞急性淋巴细胞白血病儿童和成人患者

Myers, Regina M; DiNofia, Amanda M; Li, Yimei; Diorio, Caroline; Liu, Hongyan; Wertheim, Gerald; Fraietta, Joseph A; Gonzalez, Vanessa; Plesa, Gabriela; Siegel, Donald L; Iannone, Emma; Shinehouse, Laura; Brogdon, Jennifer L; Taylor, Clare; Jadlowsky, Julie K; Hexner, Elizabeth O; Engels, Boris; Baniewicz, Diane; Callahan, Colleen; Ruella, Marco; Aplenc, Richard; Barz Leahy, Allison; McClory, Susan E; Rheingold, Susan R; Wray, Lisa; June, Carl H; Maude, Shannon L; Frey, Noelle V; Grupp, Stephan A

D3-GPC2-Directed CAR T Cells Are Safe and Efficacious in Preclinical Models of Neuroblastoma and Small Cell Lung Cancer.

D3-GPC2 靶向 CAR T 细胞在神经母细胞瘤和小细胞肺癌的临床前模型中安全有效。

Giudice Anna Maria, Matlaga Stephanie, Roth Sydney L, Gladney Whitney, Groff David, Hofmann Ted J, McDaid Kendra S, Pascual-Pasto Guillem, McIntyre Brendan, Zecchino Vincent, Martinez Dan, Spear Timothy T, Wolpaw Adam J, Assenmacher Charles-Antoine, Radaelli Enrico, Pogoriler Jenny, Pawel Bruce, Barrett David, Grupp Stephan A, Maris John M, Bosse Kristopher R

Therapies and outcomes following extramedullary relapse of pediatric and young adult ALL after CD19 CAR T-cell therapy

CD19 CAR T 细胞疗法治疗后儿童和青少年急性淋巴细胞白血病髓外复发的治疗及预后

Friedes, Barbara D; DiNofia, Amanda M; Iannone, Emma; Li, Yimei; Rheingold, Susan R; Leahy, Allison Barz; Wray, Lisa; Callahan, Colleen; Baniewicz, Diane; Vernau, Lauren; Getz, Kelly D; Aplenc, Richard; Maude, Shannon L; Grupp, Stephan A; Myers, Regina M

Real-world data for tisagenlecleucel in patients with R/R B-ALL: subgroup analyses from the CIBMTR registry

tisagenlecleucel治疗复发/难治性B细胞急性淋巴细胞白血病患者的真实世界数据:来自CIBMTR注册研究的亚组分析

John, Samuel; Curran, Kevin J; Hall, Erin M; Keating, Amy K; Baumeister, Susanne H C; Nikiforow, Sarah; Driscoll, Timothy; Moskop, Amy; McNerney, Kevin O; Phillips, Christine L; Pulsipher, Michael A; Hsieh, Emily M; Rouce, Rayne H; Pasquini, Marcelo C; Tiwari, Ranjan; Willert, Jennifer; Ramos, Roberto; Krueger, Joerg; Guest, Erin; Grupp, Stephan A

Evaluation of in vivo CAR transgene levels in tisagenlecleucel-treated patients with relapsed/refractory B-ALL and DLBCL

评估接受tisagenlecleucel治疗的复发/难治性B细胞急性淋巴细胞白血病(B-ALL)和弥漫性大B细胞淋巴瘤(DLBCL)患者体内CAR转基因水平

Awasthi, Rakesh; Grupp, Stephan A; Waldron, Edward R; Yanik, Gregory A; Tam, Constantine S; Rives, Susana; McGuirk, Joseph P; Pulsipher, Michael A; Jaeger, Ulrich; Myers, Gary D; Borchmann, Peter; Schuster, Stephen J; Stefanski, Heather E; Bishop, Michael R; Chakraborty, Abhijit; Masood, Aisha; Baruchel, André; Waller, Edmund K