Uninterrupted CAG repeat drives striatum-selective transcriptionopathy and nuclear pathogenesis in human Huntingtin BAC mice
不间断的CAG重复序列驱动人类亨廷顿蛋白BAC小鼠纹状体选择性转录病变和核病变
期刊:Neuron
影响因子:14.7
doi:10.1016/j.neuron.2022.01.006
Xiaofeng Gu ,Jeffrey Richman ,Peter Langfelder ,Nan Wang ,Shasha Zhang ,Monica Bañez-Coronel ,Huei-Bin Wang ,Lucia Yang ,Lalini Ramanathan ,Linna Deng ,Chang Sin Park ,Christopher R Choi ,Jeffrey P Cantle ,Fuying Gao ,Michelle Gray ,Giovanni Coppola ,Gillian P Bates ,Laura P W Ranum ,Steve Horvath ,Christopher S Colwell ,X William Yang