Reduction in kidney function decline and risk of severe clinical events in agalsidase beta-treated Fabry disease patients: a matched analysis from the Fabry Registry
阿加糖酶β治疗可降低法布里病患者肾功能下降和严重临床事件风险:来自法布里病登记处的匹配分析
期刊:Clinical Kidney Journal
影响因子:4.6
doi:10.1093/ckj/sfae194
Batista, Julie L; Hariri, Ali; Maski, Manish; Richards, Susan; Gudivada, Badari; Raynor, Lewis A; Ponce, Elvira; Wanner, Christoph; Desnick, Robert J