日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Using muscle homing peptide CyPep10 to deliver phosphorodiamidate morpholino oligomers in the mdx mouse.

利用肌肉归巢肽CyPep10将磷酰二胺吗啉寡聚体递送至mdx小鼠体内

Schneider Anne-Fleur E, Tanganyika-de Winter Christa L, Jirka Silvana M G, Tan Xuyu, Thompson Emily G, Ha Kristen, Mitra Anindita, Garcia Stephanie, Luimes Marleen, Oliver Ryan A, Guerlavais Vincent, Aartsma-Rus Annemieke

Splicing correction by peptide-conjugated morpholinos as a novel treatment for late-onset Pompe disease.

利用肽偶联吗啉代寡核苷酸进行剪接校正,作为治疗晚发型庞贝病的新方法

Oliver Ryan A, Ahern Meghan E, Castaneda Perla G, Jinadasa Tushare, Bardhan Anirban, Morgan Kathy Y, Ha Kristin, Adhikari Kailash, Jungels Nino, Liberman Noa, Mitra Anindita, Greer Christopher D, Wright Alec M, Thompson Emily G, Garcia Stephanie, Copson Elena, Allu Senkara, Tan Xuyu, Callahan Alex J, Cai Bao Zhong, Guerlavais Vincent, Kim Kevin J, Malmberg Annika B

Correction: Phase I Trial of ALRN-6924, a Dual Inhibitor of MDMX and MDM2, in Patients with Solid Tumors and Lymphomas Bearing Wild-type TP53

更正:ALRN-6924(一种MDMX和MDM2双重抑制剂)在携带野生型TP53的实体瘤和淋巴瘤患者中的I期试验

Saleh, Mansoor N; Patel, Manish R; Bauer, Todd M; Goel, Sanjay; Falchook, Gerald S; Shapiro, Geoffrey I; Chung, Ki Y; Infante, Jeffrey R; Conry, Robert M; Rabinowits, Guilherme; Hong, David S; Wang, Judy S; Steidl, Ulrich; Walensky, Loren D; Naik, Gurudatta; Guerlavais, Vincent; Vukovic, Vojislav; Annis, D Allen; Aivado, Manuel; Meric-Bernstam, Funda

Pharmacologic Activation of p53 Triggers Viral Mimicry Response Thereby Abolishing Tumor Immune Evasion and Promoting Antitumor Immunity

p53的药理学激活可触发病毒模拟反应,从而消除肿瘤免疫逃逸并促进抗肿瘤免疫。

Zhou, Xiaolei; Singh, Madhurendra; Sanz Santos, Gema; Guerlavais, Vincent; Carvajal, Luis A; Aivado, Manuel; Zhan, Yue; Oliveira, Mariana M S; Westerberg, Lisa S; Annis, D Allen; Johnsen, John Inge; Selivanova, Galina

Phase 1 Trial of ALRN-6924, a Dual Inhibitor of MDMX and MDM2, in Patients with Solid Tumors and Lymphomas Bearing Wild-type TP53

ALRN-6924(一种MDMX和MDM2双重抑制剂)在携带野生型TP53的实体瘤和淋巴瘤患者中的I期临床试验

Saleh, Mansoor N; Patel, Manish R; Bauer, Todd M; Goel, Sanjay; Falchook, Gerald S; Shapiro, Geoffrey I; Chung, Ki Y; Infante, Jeffrey R; Conry, Robert M; Rabinowits, Guilherme; Hong, David S; Wang, Judy S; Steidl, Ulrich; Naik, Gurudatta; Guerlavais, Vincent; Vukovic, Vojislav; Annis, D Allen; Aivado, Manuel; Meric-Bernstam, Funda

Dual inhibition of MDMX and MDM2 as a therapeutic strategy in leukemia

MDMX 和 MDM2 双重抑制作为白血病治疗策略

Carvajal, Luis A; Neriah, Daniela Ben; Senecal, Adrien; Benard, Lumie; Thiruthuvanathan, Victor; Yatsenko, Tatyana; Narayanagari, Swathi-Rao; Wheat, Justin C; Todorova, Tihomira I; Mitchell, Kelly; Kenworthy, Charles; Guerlavais, Vincent; Annis, D Allen; Bartholdy, Boris; Will, Britta; Anampa, Jesus D; Mantzaris, Ioannis; Aivado, Manuel; Singer, Robert H; Coleman, Robert A; Verma, Amit; Steidl, Ulrich