日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Height, weight, and body mass index trajectories and their correlation with functional outcome assessments in boys with Duchenne muscular dystrophy

杜氏肌营养不良症男孩的身高、体重和体质指数变化轨迹及其与功能结果评估的相关性

Schiava, Marianela; Dang, Utkarsh J; Wood, Claire; Wong, Sze Choong; Ward, Leanne M; Lofra, Robert Muni; Mayhew, Anna; Martens, William B; Gregory, Stephanie; Griggs, Robert C; Guglieri, Michela

Assessing the Relationship of Quality of Life With Functional Status in a Large Cohort of Adult Patients With Neuromuscular Disorders

评估大量成年神经肌肉疾病患者的生活质量与功能状态的关系

Wong, Karen S W; Sen, Anando; Michell-Sodhi, Jassi; Moat, Dionne; McCallum, Michelle; Richardson, Mark; Harris, Elizabeth; Mayhew, Anna G; Guglieri, Michela; Grover, Emma; Diaz-Manera, Jordi; Robinson, Emma; Elseed, Maha; Mason, Joseph; Geagan, Chloe; James, Meredith K; Straub, Volker; Marini-Bettolo, Chiara; Muni-Lofra, Robert

Evaluation of a serum protein signature as monitoring biomarker for Duchenne Muscular Dystrophy in a long-term clinical trial with corticosteroids

在长期皮质类固醇临床试验中,评估血清蛋白特征作为杜氏肌营养不良症监测生物标志物的价值

Degan, Chiara; Tobin, Rebecca A; de Vries, Sharon I; Jiménez-Requena, Albert; Peco, Amela; Guglieri, Michela; Diaz-Manera, Jordi; van der Burgt, Yuri E M; Vlijmen, Bart J M; Hathout, Yetrib; Szigyarto, Cristina Al-Khalili; Dang, Utkarsh J; Tsonaka, Roula; Spitali, Pietro

Assessing Potential Valve-Preserving Effects of SGLT2 Inhibitors in Degenerative Aortic Stenosis: A Propensity-Matched Study

评估SGLT2抑制剂在退行性主动脉瓣狭窄中的潜在瓣膜保护作用:一项倾向性匹配研究

Morel, Olivier; Guglieri, Michael; Trimaille, Antonin; Marchandot, Benjamin; Bisson, Arnaud; Granier, Amandine; Schini-Kerth, Valérie; Bernard, Anne; Fauchier, Laurent

Quality of care delivery in patients with acute heart failure

急性心力衰竭患者的医疗服务质量

Guglieri, Mickael; Genet, Thibaud; Fauchier, Laurent

Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons

吉维诺司他治疗杜氏肌营养不良症的长期疗效评价及自然病程比较

McDonald, Craig M; Guglieri, Michela; Vučinić, Dragana; Acsadi, Gyula; Brandsema, John F; Bruno, Claudio; Finanger, Erika L; Harper, Amy; Lobato, Mercedes Lopez; Masson, Riccardo; Muelas, Nuria; Munell, Francina; Nevo, Yoram; Péréon, Yann; Phan, Han; Sansone, Valeria A; Scoto, Mariacristina; Willis, Tracey; Finkel, Richard S; Vandenborne, Krista; Cazzaniga, Sara; Montrasio, Silvia; Alessi, Federica; Bettica, Paolo; Mercuri, Eugenio

Predicting trajectories of the north star ambulatory assessment total score in Duchenne muscular dystrophy

预测杜氏肌营养不良症患者北极星步行评估总分的轨迹

Muntoni, Francesco; Signorovitch, James; Goemans, Nathalie; Manzur, Adnan Y; Done, Nicolae; Sajeev, Gautam; Li, Jiayang; Akbarnejad, Hanane; Sharma, Aarushi; Ward, Susan J; Niks, Erik H; Servais, Laurant; Mercuri, Eugenio; Guglieri, Michela; Straub, Volker; de Groot, Imelda; Ridout, Deborah; McDonald, Craig

Development of a guideline for orthopaedic management in the care of children and young people with Duchenne muscular dystrophy in the UK National Health Service

英国国家医疗服务体系 (NHS) 制定杜氏肌营养不良症儿童和青少年骨科治疗指南

Henman, Philip D; Turner, Catherine; Aird, James; Atherton, William Guy; Campbell, Donald; Carpenter, Clare; Carsi, Maria Belen; Dixon, Melville; Giannakakis, Nikolaos; Girdler-Hardy, Thomas; Hulme, Alison; James, Meredith; Joseph, Shuko; Kiely, Nigel T; Ohly, Kirsty; Porter, Anna; Rad, Darius; Reuben, Emily; Walton, Roger; Wong, Sze Choong; Guglieri, Michela

Translational kinetic-pharmacodynamics of mRNA-6231, an investigational mRNA therapeutic encoding mutein interleukin-2

mRNA-6231(一种编码突变型白细胞介素-2的在研mRNA疗法)的转化动力学-药效学研究

Ivana Liric Rajlic ,Beatriz Guglieri-Lopez ,Nabeel Rangoonwala ,Vijay Ivaturi ,Linh Van ,Simone Mori ,Brian Wipke ,Douglas Burdette ,Husain Attarwala

Translational kinetic-pharmacodynamics of mRNA-6231, an investigational mRNA therapeutic encoding mutein interleukin-2

mRNA-6231(一种编码突变型白细胞介素-2的在研mRNA疗法)的转化动力学-药效学研究

Ivana Liric Rajlic,Beatriz Guglieri-Lopez,Nabeel Rangoonwala,Vijay Ivaturi,Linh Van,Simone Mori,Brian Wipke,Douglas Burdette,Husain Attarwala