Long-Term Evaluation of Givinostat in Duchenne Muscular Dystrophy, and Natural History Comparisons
吉维诺司他治疗杜氏肌营养不良症的长期疗效评价及自然病程比较
期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.70165
McDonald, Craig M; Guglieri, Michela; Vučinić, Dragana; Acsadi, Gyula; Brandsema, John F; Bruno, Claudio; Finanger, Erika L; Harper, Amy; Lobato, Mercedes Lopez; Masson, Riccardo; Muelas, Nuria; Munell, Francina; Nevo, Yoram; Péréon, Yann; Phan, Han; Sansone, Valeria A; Scoto, Mariacristina; Willis, Tracey; Finkel, Richard S; Vandenborne, Krista; Cazzaniga, Sara; Montrasio, Silvia; Alessi, Federica; Bettica, Paolo; Mercuri, Eugenio