日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity.

聚焦超声可显著扩大 AAV 递送的 Cas9 的分布和活性

Gumusgoz Emrah, Kasiri Sahba, Youssef Ibrahim, Verma Mayank, Chopra Rajiv, Villarreal Acha Daniel, Wu Jun, Marriam Ummay, Alao Esther, Chen Xin, Guisso Dikran R, Gray Steven J, Shah Bhavya R, Minassian Berge A

AAV-Mediated Artificial miRNA Reduces Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models

AAV介导的人工miRNA可减少成年多聚葡萄糖体病和拉福拉病小鼠模型中的致病性多聚葡萄糖体和神经炎症

Gumusgoz, Emrah; Kasiri, Sahba; Guisso, Dikran R; Wu, Jun; Dear, Matthew; Verhalen, Brandy; Minassian, Berge A

Targeting Gys1 with AAV-SaCas9 Decreases Pathogenic Polyglucosan Bodies and Neuroinflammation in Adult Polyglucosan Body and Lafora Disease Mouse Models

利用 AAV-SaCas9 靶向 Gys1 可减少成年多聚葡糖体病和拉福拉病小鼠模型中的致病性多聚葡糖体和神经炎症

Gumusgoz, Emrah; Guisso, Dikran R; Kasiri, Sahba; Wu, Jun; Dear, Matthew; Verhalen, Brandy; Nitschke, Silvia; Mitra, Sharmistha; Nitschke, Felix; Minassian, Berge A

The antioxidant MnTBAP does not effectively downregulate CD4 expression in T cells in vivo

抗氧化剂MnTBAP在体内并不能有效下调T细胞中CD4的表达。

Manouchehri, Navid; Guisso, Dikran R; Hussain, Rehana Z; Minassian, Berge A; Stüve, Olaf