日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Experimental Galactose-1-Phosphate Uridylyltransferase (GALT) mRNA Therapy Improves Motor-Related Phenotypes in a Mouse Model of Classic Galactosemia-A Pilot Study

实验性半乳糖-1-磷酸尿苷酰转移酶 (GALT) mRNA 疗法改善经典半乳糖血症小鼠模型的运动相关表型——一项初步研究

Bellagamba, Olivia; Guo, Aaron J; Yan, Xinhua; Sarkis, Joe; Balakrishnan, Bijina; Lai, Kent

Assessment of Long-Term Safety and Efficacy of Purple Sweet Potato Color (PSPC) and Myo-Inositol (MI) Treatment for Motor Related and Behavioral Phenotypes in a Mouse Model of Classic Galactosemia.

评估紫薯色素 (PSPC) 和肌醇 (MI) 治疗对经典半乳糖血症小鼠模型运动相关和行为表型的长期安全性和有效性

Bellagamba Olivia, Guo Aaron J, Senthilkumar Sandhya, Lillevik Synneva Hagen, De Biase Davide, Lai Kent, Balakrishnan Bijina