Astroglial conditional Slc13a3 knockout is therapeutic in murine Canavan leukodystrophy
星形胶质细胞条件性Slc13a3敲除对小鼠卡纳万脑白质营养不良症具有治疗作用
期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.52010
Hull, Vanessa L; Wang, Yan; McDonough, Jennifer; Zhu, Meina; Burns, Travis; Al Ramel, Najmah; Dehghani, Ali; Guo, Fuzheng; Pleasure, David