日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.

AAV基因疗法治疗杜氏肌营养不良症:EMBARK 3期随机试验

Mendell Jerry R, Muntoni Francesco, McDonald Craig M, Mercuri Eugenio M, Ciafaloni Emma, Komaki Hirofumi, Leon-Astudillo Carmen, Nascimento Andrés, Proud Crystal, Schara-Schmidt Ulrike, Veerapandiyan Aravindhan, Zaidman Craig M, Guridi Maitea, Murphy Alexander P, Reid Carol, Wandel Christoph, Asher Damon R, Darton Eddie, Mason Stefanie, Potter Rachael A, Singh Teji, Zhang Wenfei, Fontoura Paulo, Elkins Jacob S, Rodino-Klapac Louise R

Exploring the natural history of bone mineral density in Duchenne muscular dystrophy: a systematic literature review

探索杜氏肌营养不良症患者骨矿物质密度的自然史:系统性文献综述

De Ford, Christian; Guridi, Maitea; Chen, Yingjia; Murphy, Alexander P; Wood, Claire; McMillan, Hugh J; Mercuri, Eugenio; Crabtree, Nicola; Ward, Leanne

The Clinical Development of Taldefgrobep Alfa: An Anti-Myostatin Adnectin for the Treatment of Duchenne Muscular Dystrophy

Taldefgrobep Alfa 的临床开发:一种用于治疗杜氏肌营养不良症的抗肌肉生长抑制素 Adnectin

Muntoni, Francesco; Byrne, Barry J; McMillan, Hugh J; Ryan, Monique M; Wong, Brenda L; Dukart, Juergen; Bansal, Amita; Cosson, Valerie; Dreghici, Roxana; Guridi, Maitea; Rabbia, Michael; Staunton, Hannah; Tirucherai, Giridhar S; Yen, Karl; Yuan, Xiling; Wagner, Kathryn R

Stride Velocity 95th Centile: Insights into Gaining Regulatory Qualification of the First Wearable-Derived Digital Endpoint for use in Duchenne Muscular Dystrophy Trials

步速第95百分位:首个用于杜氏肌营养不良症试验的可穿戴设备衍生数字终点指标获得监管认证的见解

Servais, Laurent; Yen, Karl; Guridi, Maitea; Lukawy, Jacek; Vissière, David; Strijbos, Paul

Alterations to mTORC1 signaling in the skeletal muscle differentially affect whole-body metabolism

骨骼肌中 mTORC1 信号通路的改变对全身代谢的影响各不相同

Guridi, Maitea; Kupr, Barbara; Romanino, Klaas; Lin, Shuo; Falcetta, Denis; Tintignac, Lionel; Rüegg, Markus A

Antioxidant peroxiredoxin 6 protein rescues toxicity due to oxidative stress and cellular hypoxia in vitro, and attenuates prion-related pathology in vivo

抗氧化过氧化物酶6蛋白可在体外挽救氧化应激和细胞缺氧引起的毒性,并在体内减轻朊病毒相关病理。

Asuni, Ayodeji A; Guridi, Maitea; Sanchez, Sandrine; Sadowski, Martin J

Clonal Mature Adipocyte Production of Proliferative-competent Daughter Cells Requires Lipid Export Prior to Cell Division

克隆成熟脂肪细胞产生具有增殖能力的子细胞需要细胞分裂前进行脂质输出。

Chen, Jie; Guridi, Maitea; Fernyhough, Melinda E; Jiang, Zhihua; Guan, LeLuo; Hausman, Gary J; Dodson, Michael V