日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Health Care Utilization Databases obtained from health system inform outcome for ruxolitinib treatment in patients with myelofibrosis

从医疗系统获取的医疗保健利用数据库可用于评估鲁索替尼治疗骨髓纤维化患者的疗效。

Mora, Barbara; Franchi, Matteo; Margotto, Ludovica; Leoni, Olivia; D'ippoliti, Daniela; Carloni, Emanuela; Cozzi, Ilaria; Santelli, Enrica; Gemmi, Fabrizio; Szasz, Claudia; Maffioli, Margherita; Gurnari, Carmelo; Attardi, Enrico; Cattaneo, Daniele; Bortolotti, Marta; Fracchiolla, Nicola Stefano; Iurlo, Alessandra; Corrao, Giovanni; Della Porta, Matteo Giovanni; Vannucchi, Alessandro Maria; Voso, Maria Teresa; Guglielmelli, Paola; Passamonti, Francesco

American College of Rheumatology Guidance Statement for Diagnosis and Management of VEXAS Developed by the International VEXAS Working Group Expert Panel

美国风湿病学会关于VEXAS诊断和治疗的指导声明,由国际VEXAS工作组专家组制定

Mekinian, Arsene; Georgin-Lavialle, Sophie; Ferrada, Marcela A; Savic, Sinisa; Koster, Matthew J; Kosmider, Olivier; Comont, Thibault; Heiblig, Mael; Arostegui, Juan I; Bosco, Annmarie; Bourguiba, Rim; Calvo, Katherine R; Cargo, Catherine; Cattaneo, Chiara; Chasset, François; Coelho, Henrique; Campochiaro, Corrado; Crisafulli, Francesca; Ducharme-Benard, Stephanie; Faria, Raquel; Franceschini, Franco; Frassi, Micol; Groarke, Emma M; Gurnari, Carmelo; Hakobyan, Yervand; Jamilloux, Yvan; Jurcut, Ciprian; Kirino, Yohei; Kulasekararaj, Austin; Kunimoto, Hiroyoshi; Madigan, Lauren M; Mann, Heřman F; Marvisi, Chiara; Milchert, Marcin; Morais, Sara; Sockel, Katja; Muratore, Francesco; Nakajima, Hideaki; Patnaik, Mrinal M; Regadas, Luísa; Robin, Marie; Rutgers, Abraham; Salvarani, Carlo; Sammel, Anthony M; Seebach, Joerg; Sujobert, Pierre; Tomelleri, Alessandro; Urbanski, Geoffrey; Vandergheynst, Frédéric; Vieira, Romana; Viswanatha, David S; Więsik-Szewczyk, Ewa; Diral, Elisa; Terrier, Benjamin; Patel, Bhavisha A; Fenaux, Pierre; Grayson, Peter C; Beck, David B

Recurrent fever and association with severe organ involvement, mortality and treatment outcomes in VEXAS syndrome: data from the AIDA Network

VEXAS综合征中反复发热与严重器官受累、死亡率和治疗结果的相关性:来自AIDA网络的数据

Caggiano, Valeria; Sbalchiero, Jessica; Frassi, Micol; Crisafulli, Francesca; Cavazzana, Ilaria; Hinojosa-Azaola, Andrea; Martín-Nares, Eduardo; Guaracha-Basañez, Guillermo Arturo; Torres-Ruiz, Jiram; Wiesik-Szewczyk, Ewa; Nowakowska-Plaza, Anna; Sfriso, Paolo; Bindoli, Sara; Rizzo, Samuele; Hernández-Rodríguez, José; Gómez-Caverzaschi, Verónica; Araújo, Olga; Mayrink Giardini, Henrique A; González-García, Andrés; Lopalco, Giuseppe; Viapiana, Ombretta; Bixio, Riccardo; Tufan, Abdurrahman; Hissaria, Pravin; Beecher, Mark; Callisto, Alicia; De Paulis, Amato; Dagna, Lorenzo; Campochiaro, Corrado; Tomelleri, Alessandro; Bugatti, Serena; Milanesi, Alessandra; Ruiz-Irastorza, Guillermo; Soto-Peleteiro, Adriana; Piga, Matteo; Cauli, Alberto; Conti, Fabrizio; Cardamone, Chiara; Triggianese, Paola; Gurnari, Carmelo; Vitetta, Rosetta; Prete, Marcella; Racanelli, Vito; Talarico, Rosaria; Ferro, Francesco; di Cianni, Federica; Cuccaro, Maria Chiara; Mayo-Juanatey, Adrián; Renieri, Alessandra; Sorrentino, Vincenzo; Ergun, Mehmet Ali; Balistreri, Alberto; Frediani, Bruno; Bocchia, Monica; Fabiani, Claudia; Cantarini, Luca; Vitale, Antonio

PAXIS: A Randomized, Double-Blind, Placebo-Controlled, Dose-Finding Phase 2 Study (Part 1) Followed by an Open-Label Period (Part 2) to Assess the Efficacy and Safety of Pacritinib in Patients with VEXAS Syndrome

PAXIS:一项随机、双盲、安慰剂对照、剂量探索性 II 期研究(第一部分)及后续开放标签期(第二部分),旨在评估帕克替尼治疗 VEXAS 综合征患者的疗效和安全性

Beck, David B; Heiblig, Maël; Savic, Sinisa; Ferrada, Marcela A; Mekinian, Arsène; Chowdhury, Onima; Hammond, Danielle; Weeks, Lachelle D; Gurnari, Carmelo; Kirino, Yohei; Georgin-Lavialle, Sophie; Buckley, Sarah A; Garcha, Raman; Harder, Bryan G; Koster, Matthew J

Maladaptive somatic gene rescue as predisposition to JAK2 molecular abnormalities? Insights from an Israeli family

适应不良的体细胞基因拯救是否会导致JAK2分子异常?来自一个以色列家族的启示

Borsani, Oscar; Gurnari, Carmelo; Pietra, Daniela; Rumi, Elisa

Inborn errors of immunity underlie clonal T cell expansions in large granular lymphocyte leukemia

先天性免疫缺陷是大颗粒淋巴细胞白血病中克隆性T细胞扩增的根本原因。

Bravo-Perez, Carlos; Gurnari, Carmelo; Huuhtanen, Jani; Kawashima, Naomi; Guarnera, Luca; Mandala, Aashray; Williams, Nakisha D; Haddad, Christopher; Witt, Michaela; Unlu, Serhan; Brady, Zachary; Ogbue, Olisaemeka; Orland, Mark; Ahmed, Arooj; Kubota, Yasuo; Pagliuca, Simona; Durmaz, Arda; Mustjoki, Satu; Visconte, Valeria; Maciejewski, Jaroslaw P

Non canonical c-CBL mutations define a specific phenotype of myeloid neoplasia

非典型 c-CBL 突变定义了髓系肿瘤的一种特定表型

Guarnera, Luca; Gurnari, Carmelo; Bravo-Perez, Carlos; Durmaz, Arda; Williams, Nakisha D; Awada, Hussein; Kawashima, Naomi; Ahmed, Arooj; Unlu, Serhan; Ogbue, Olisaemeka D; Haddad, Christopher; Mandala, Aashray; Kubota, Yasuo; Bodo, Juraj; Crane, Genevieve M; Rogers, Heesun J; Maciejewski, Jaroslaw P; Visconte, Valeria

Exploring patient-reported outcomes and morbidity burden of patients with VEXAS syndrome: a scoping review

探索VEXAS综合征患者的患者报告结局和发病负担:一项范围界定综述

Efficace, Fabio; Krepper, Daniela; Sparano, Francesco; Fazi, Paola; Voso, Maria Teresa; Gurnari, Carmelo

Elderly Patients With Aplastic Anemia: Treatment Patterns and Outcomes in the Real World

老年再生障碍性贫血患者:真实世界中的治疗模式和结果

Fattizzo, Bruno; Gurnari, Carmelo; Giammarco, Sabrina; Ricchiuti, Antony; Awada, Hussein; Bortolotti, Marta; Galli, Nicole; Pedone, Giacinto Luca; Versino, Francesco; Consonni, Dario; Trikha, Roochi; Gandhi, Shreyans; Sica, Simona; Maciejewski, Jaroslaw P; Kulasekararaj, Austin; Barcellini, Wilma

Efficacy and safety profile of biotechnological agents and Janus kinase inhibitors in VEXAS syndrome: data from the international AIDA Network VEXAS registry

生物技术药物和 Janus 激酶抑制剂治疗 VEXAS 综合征的疗效和安全性:来自国际 AIDA 网络 VEXAS 注册研究的数据

Vitale, Antonio; Caggiano, Valeria; Leone, Flavia; Hinojosa-Azaola, Andrea; Martín-Nares, Eduardo; Guaracha-Basañez, Guillermo Arturo; Torres-Ruiz, Jiram; Kawakami-Campos, Perla Ayumi; Hissaria, Pravin; Callisto, Alicia; Beecher, Mark; Dagna, Lorenzo; Campochiaro, Corrado; Tomelleri, Alessandro; Frassi, Micol; Franceschini, Franco; Crisafulli, Francesca; Hernández-Rodríguez, José; Gómez-Caverzaschi, Verónica; Araújo, Olga; Sfriso, Paolo; Bindoli, Sara; Baggio, Chiara; Sota, Jurgen; Tufan, Abdurrahman; Kucuk, Hamit; Piga, Matteo; Cauli, Alberto; D'Agostino, Maria Antonietta; De Paulis, Amato; Mormile, Ilaria; Giardini, Henrique A Mayrink; Cordeiro, Rafael Alves; Lopalco, Giuseppe; Iannone, Florenzo; Monti, Sara; Montecucco, Carlomaurizio; Ruiz-Irastorza, Guillermo; Soto-Peleteiro, Adriana; Triggianese, Paola; Gurnari, Carmelo; Viapiana, Ombretta; Bixio, Riccardo; Vitetta, Rosetta; Rovera, Guido; Conticini, Edoardo; La Torre, Francesco; Portincasa, Piero; Jaber, Nour; Ragab, Gaafar; Maher, Amina; Batu, Ezgi Deniz; Ozen, Seza; Wiesik-Szewczyk, Ewa; de-la-Torre, Alejandra; Balistreri, Alberto; Frediani, Bruno; Fabiani, Claudia; Cantarini, Luca