Chimeric siRNAs with chemically modified pentofuranose and hexopyranose nucleotides: altritol-nucleotide (ANA) containing GalNAc-siRNA conjugates: in vitro and in vivo RNAi activity and resistance to 5'-exonuclease
具有化学修饰的戊呋喃糖和己吡喃糖核苷酸的嵌合 siRNA:含有 GalNAc-siRNA 结合物的阿卓糖醇核苷酸 (ANA):体外和体内 RNAi 活性和对 5'-外切酶的抗性
期刊:Nucleic Acids Research
影响因子:16.6
doi:10.1093/nar/gkaa125
Pawan Kumar, Rohan Degaonkar, Dale C Guenther, Mikhail Abramov, Guy Schepers, Marie Capobianco, Yongfeng Jiang, Joel Harp, Charalambos Kaittanis, Maja M Janas, Adam Castoreno, Ivan Zlatev, Mark K Schlegel, Piet Herdewijn, Martin Egli, Muthiah Manoharan