Mechanism-based combination treatment dramatically increases therapeutic efficacy in murine globoid cell leukodystrophy.
基于机制的联合治疗显著提高了小鼠球状细胞脑白质营养不良的治疗效果
期刊:Journal of Neuroscience
影响因子:4
doi:10.1523/JNEUROSCI.4199-14.2015
Hawkins-Salsbury Jacqueline A, Shea Lauren, Jiang Xuntian, Hunter Daniel A, Guzman A Miguel, Reddy Adarsh S, Qin Elizabeth Y, Li Yedda, Gray Steven J, Ory Daniel S, Sands Mark S