日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Divalent siRNA for prion disease

用于朊病毒病的二价siRNA

Gentile, Juliana E; Corridon, Taylor L; Serack, Fiona E; Echeverria, Dimas; Kennedy, Zachary C; Gallant-Behm, Corrie L; Hassler, Matthew R; Kinberger, Garth A; Kelemen, Margaret N; Kamath, Nikita G; Lian, Yuan; Gross, Katherine Y; Miller, Rachael; DeSouza-Lenz, Kendrick; Howard, Michael; Guzman, Kenia; Chan, Nathan; Laversenne, Vanessa; Curtis, Daniel; Fettes, Kevin; Lemaitre, Marc; Jackson, Aimee L; Yamada, Ken; Alterman, Julia F; Coffey, Alissa A; Minikel, Eric Vallabh; Khvorova, Anastasia; Vallabh, Sonia M

Divalent siRNA for prion disease.

用于朊病毒病的二价siRNA。

Gentile Juliana E, Corridon Taylor L, Serack Fiona E, Echeverria Dimas, Kennedy Zachary C, Gallant-Behm Corrie L, Hassler Matthew R, Kinberger Garth A, Kelemen Margaret N, Kamath Nikita G, Lian Yuan, Gross Katherine Y, Miller Rachael, DeSouza-Lenz Kendrick, Howard Michael, Guzman Kenia, Chan Nathan, Laversenne Vanessa, Curtis Daniel T, Fettes Kevin, Lemaitre Marc, Jackson Aimee L, Yamada Ken, Alterman Julia F, Coffey Alissa A, Minikel Eric Vallabh, Khvorova Anastasia, Vallabh Sonia M

Author Correction: In vivo base editing extends lifespan of a humanized mouse model of prion disease

作者更正:体内碱基编辑延长了朊病毒病人源化小鼠模型的寿命

An, Meirui; Davis, Jessie R; Levy, Jonathan M; Serack, Fiona E; Harvey, John W; Brauer, Pamela P; Pirtle, Catherine P; Berríos, Kiara N; Newby, Gregory A; Yeh, Wei-Hsi; Kamath, Nikita; Mortberg, Meredith; Lian, Yuan; Howard, Michael; DeSouza-Lenz, Kendrick; Guzman, Kenia; Thai, Aaron; Graffam, Samantha; Laversenne, Vanessa; Coffey, Alissa A; Frei, Jeannine; Pierce, Sarah E; Safar, Jiri G; Deverman, Benjamin E; Minikel, Eric Vallabh; Vallabh, Sonia M; Liu, David R

In vivo base editing extends lifespan of a humanized mouse model of prion disease.

体内碱基编辑延长了朊病毒疾病人源化小鼠模型的寿命

An Meirui, Davis Jessie R, Levy Jonathan M, Serack Fiona E, Harvey John W, Brauer Pamela P, Pirtle Catherine P, Berríos Kiara N, Newby Gregory A, Yeh Wei-Hsi, Kamath Nikita, Mortberg Meredith, Lian Yuan, Howard Michael, DeSouza-Lenz Kendrick, Guzman Kenia, Thai Aaron, Graffam Samantha, Laversenne Vanessa, Coffey Alissa A, Frei Jeannine, Pierce Sarah E, Safar Jiri G, Deverman Benjamin E, Minikel Eric Vallabh, Vallabh Sonia M, Liu David R

Evidence that minocycline treatment confounds the interpretation of neurofilament as a biomarker.

有证据表明,米诺环素治疗会混淆神经丝作为生物标志物的解释

Gentile Juliana E, Heiss Christina N, Corridon Taylor L, Mortberg Meredith A, Fruhwürth Stefanie, Guzman Kenia, Grötschel Lana, Montoliu-Gaya Laia, Chan Kwan, Herring Neil C, Janicki Timothy, Nhass Rajaa, Manavala Sarathy Janani, Erickson Brian, Kunz Ryan, Erickson Alison, Braun Craig, Henry Katherine T, Bry Lynn, Arnold Steven E, Vallabh Minikel Eric, Zetterberg Henrik, Vallabh Sonia M

Evidence that minocycline treatment confounds the interpretation of neurofilament as a biomarker

有证据表明,米诺环素治疗会干扰神经丝作为生物标志物的解读。

Gentile, Juliana E; Heiss, Christina; Corridon, Taylor L; Mortberg, Meredith A; Fruhwürth, Stefanie; Guzman, Kenia; Grötschel, Lana; Chan, Kwan; Herring, Neil C; Janicki, Timothy; Nhass, Rajaa; Sarathy, Janani Manavala; Erickson, Brian; Kunz, Ryan; Erickson, Alison; Braun, Craig; Henry, Katherine T; Bry, Lynn; Arnold, Steven E; Minikel, Eric Vallabh; Zetterberg, Henrik; Vallabh, Sonia M