日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Advances in Gene Therapy for Inherited Haemoglobinopathies

遗传性血红蛋白病基因治疗进展

Gaspar, Anna B; Gaspar, H Bobby

Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant

基于抗CD45 PBD的抗体药物偶联物是基因治疗和干细胞移植的有效靶向预处理剂。

Yeung, Jenny; Liao, Aiyin; Shaw, Matthew; Silva, Soraia; Vetharoy, Winston; Rico, Diego Leon; Kirby, Ian; Zammarchi, Francesca; Havenith, Karin; de Haan, Lolke; van Berkel, Patrick H; Sebire, Neil; Ogunbiyi, Olumide K; Booth, Claire; Gaspar, H Bobby; Thrasher, Adrian J; Chester, Kerry A; Amrolia, Persis J

Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier

溶酶体贮积症中枢神经系统靶向治疗:跨越血脑屏障的药物递送策略

Critchley, Bethan J; Gaspar, H Bobby; Benedetti, Sara

Lentiviral Gene Transfer Corrects Immune Abnormalities in XIAP Deficiency

慢病毒基因转移纠正 XIAP 缺乏症的免疫异常

Joseph Topal, Neelam Panchal, Amairelys Barroeta, Anna Roppelt, Annelotte Mudde, H Bobby Gaspar, Adrian J Thrasher, Benjamin C Houghton, Claire Booth

Assessing chronic stress in wild mammals using claw-derived cortisol: a validation using European badgers (Meles meles)

利用爪部皮质醇评估野生哺乳动物的慢性应激:以欧洲獾(Meles meles)为例进行验证

Fokidis, H Bobby; Brock, Taylor; Newman, Chris; Macdonald, David W; Buesching, Christina D

Long-Term Immune Recovery After Hematopoietic Stem Cell Transplantation for ADA Deficiency: a Single-Center Experience

ADA缺陷患者接受造血干细胞移植后的长期免疫重建:单中心经验

Kreins, Alexandra Y; Velasco, Helena F; Cheong, Kai-Ning; Rao, Kanchan; Veys, Paul; Worth, Austen; Gaspar, H Bobby; Booth, Claire

Retrospective, Landmark Analysis of Long-term Adult Morbidity Following Allogeneic HSCT for Inborn Errors of Immunity in Infancy and Childhood

回顾性里程碑分析:异基因造血干细胞移植治疗婴幼儿期先天性免疫缺陷后成人长期发病率

Day, James W; Elfeky, Reem; Nicholson, Bethany; Goodman, Rupert; Pearce, Rachel; Fox, Thomas A; Worth, Austen; Booth, Claire; Veys, Paul; Carpenter, Ben; Hough, Rachael; Gaspar, H Bobby; Titman, Penny; Ridout, Deborah; Workman, Sarita; Hernandes, Fernando; Sandford, Kit; Laurence, Arian; Campbell, Mari; Burns, Siobhan O; Morris, Emma C

Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency

自体体外慢病毒基因疗法治疗腺苷脱氨酶缺乏症

Kohn, Donald B; Booth, Claire; Shaw, Kit L; Xu-Bayford, Jinhua; Garabedian, Elizabeth; Trevisan, Valentina; Carbonaro-Sarracino, Denise A; Soni, Kajal; Terrazas, Dayna; Snell, Katie; Ikeda, Alan; Leon-Rico, Diego; Moore, Theodore B; Buckland, Karen F; Shah, Ami J; Gilmour, Kimberly C; De Oliveira, Satiro; Rivat, Christine; Crooks, Gay M; Izotova, Natalia; Tse, John; Adams, Stuart; Shupien, Sally; Ricketts, Hilory; Davila, Alejandra; Uzowuru, Chilenwa; Icreverzi, Amalia; Barman, Provaboti; Campo Fernandez, Beatriz; Hollis, Roger P; Coronel, Maritess; Yu, Allen; Chun, Krista M; Casas, Christian E; Zhang, Ruixue; Arduini, Serena; Lynn, Frances; Kudari, Mahesh; Spezzi, Andrea; Zahn, Marco; Heimke, Rene; Labik, Ivan; Parrott, Roberta; Buckley, Rebecca H; Reeves, Lilith; Cornetta, Kenneth; Sokolic, Robert; Hershfield, Michael; Schmidt, Manfred; Candotti, Fabio; Malech, Harry L; Thrasher, Adrian J; Gaspar, H Bobby

Long-term lymphoid progenitors independently sustain naïve T and NK cell production in humans

长期存在的淋巴祖细胞能够独立维持人类体内初始T细胞和NK细胞的产生。

Natalia Izotova # ,Christine Rivat # ,Cristina Baricordi ,Elena Blanco ,Danilo Pellin ,Eleanor Watt ,Athina S Gkazi ,Stuart Adams ,Kimberly Gilmour ,Jinhua Bayford ,Claire Booth ,H Bobby Gaspar ,Adrian J Thrasher ,Luca Biasco

Urban bat pups take after their mothers and are bolder and faster learners than rural pups

城市里的蝙蝠幼崽更像它们的母亲,比农村的幼崽更大胆,学习能力也更强。

Harten, Lee; Gonceer, Nesim; Handel, Michal; Dash, Orit; Fokidis, H Bobby; Yovel, Yossi