Hematopoietic stem cell transplantation for purine nucleoside phosphorylase deficiency: an EBMT-IEWP retrospective study
造血干细胞移植治疗嘌呤核苷磷酸化酶缺乏症:一项EBMT-IEWP回顾性研究
期刊:Blood
影响因子:23.1
doi:10.1182/blood.2025029640
Herrmann, Uli S; Felber, Matthias; Worth, Austen; Haskologlu, Sule; Dogu, Figen; Lewis, Victor A; Strahm, Brigitte; Groll, Andreas; Gennery, Andrew R; Hauck, Fabian; Wynn, Robert; Coussons, Mary; Meyts, Isabelle; Lindemans, Caroline; Bordon, Victoria; Bredius, Robbert G M; Kühl, Jörn-Sven; Völler, Mirjam; Zirngibl, Felix; Zaidman, Irina; Laberko, Alexandra; Zeilhofer, Ulrike; Hauri-Hohl, Mathias; Lankester, Arjan; Ikinciogullari, Aydan; Guilcher, Gregory M T; Hackenberg, Annette; Yeşilipek, Akif; Davies, Graham; Rao, Kanchan; Hershfield, Michael Steven; Parikh, Suhag H; Gilbert, Patrick; Bettoni da Cunha Riehm, Claudia; Albert, Michael H; Schulz, Ansgar S; Hönig, Manfred; Neven, Bénédicte; Güngör, Tayfun