日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficient in vivo mammalian neuron editing using peptide-mediated CRISPR enzyme delivery

利用肽介导的CRISPR酶递送实现高效的体内哺乳动物神经元编辑

Manohar, Brigette D; Travis, Meika; Munjal, Vikas; Baehr, Christopher M; Rahnama, Lily M A; Kang, Min Hyung; Haddad, Rania F; Asija, Kunica; Noel, Eric A; Peddireddy, Navya; Chouhan, Runvir S; Sharma, Rohit; Wyman, Stacia K; Krishnappa, Netravathi; Killebrew, Deirdre A; Li, Song Hua; Snow, Kathy J; Byrne, Addison K; Boosani, Chandra S; Otero, P Anthony; Bringas, John; O'Brien, Allison A; Rocco, Matthew T; Zimmerly, Madison P; Gray, Isabelle; Sran, Gunita K; Patel, Mia I; Seidensticker, Emily F; Saville, Ethan; Gaitan, Yaned; Schmelzle, Amanda L; Subramanyam, Pradeep Nag B; Samaranch, Lluis; Green, Jonathan A; Wells, Kevin D; Ehrenberg, Alexander J; Murray, Stephen A; Clelland, Claire D; Murthy, Niren; Lonser, Russell R; Hadaczek, Piotr; Van Laar, Victor S; Bankiewicz, Krystof S; Wilson, Ross C

Persistent GDNF Expression 45 Months after Putaminal Infusion of AAV2-GDNF in a Patient with Parkinson's Disease

帕金森病患者壳核内注射AAV2-GDNF 45个月后,GDNF表达持续存在

Heiss, John D; Ray-Chaudhury, Abhik; Kleiner, David E; Ehrlich, Debra J; Scott, Gretchen; Edwards, Nancy A; Goldstein, David S; Hammoud, Dima A; Hadaczek, Piotr; Van Laar, Victor S; Graff, Shantelle A; Herscovitch, Peter; Lungu, Codrin; Hallett, Mark; Lonser, Russell R; Zaghloul, Kareem A; Bankiewicz, Krystof S

Kinetics and MR-Based Monitoring of AAV9 Vector Delivery into Cerebrospinal Fluid of Nonhuman Primates

非人灵长类动物脑脊液中AAV9载体递送的动力学和基于磁共振的监测

Ohno, Kousaku; Samaranch, Lluis; Hadaczek, Piotr; Bringas, John R; Allen, Philip C; Sudhakar, Vivek; Stockinger, Diane E; Snieckus, Christopher; Campagna, Michael V; San Sebastian, Waldy; Naidoo, Jerusha; Chen, Haifeng; Forsayeth, John; Salegio, Ernesto A; Hwa, Granger G C; Bankiewicz, Krystof S

Ganglioside Metabolism and Parkinson's Disease

神经节苷脂代谢与帕金森病

Forsayeth, John; Hadaczek, Piotr

Widespread AAV1- and AAV2-mediated transgene expression in the nonhuman primate brain: implications for Huntington's disease

非人灵长类动物大脑中广泛的AAV1和AAV2介导的转基因表达:对亨廷顿病的启示

Hadaczek, Piotr; Stanek, Lisa; Ciesielska, Agnieszka; Sudhakar, Vivek; Samaranch, Lluis; Pivirotto, Philip; Bringas, John; O'Riordan, Catherine; Mastis, Bryan; San Sebastian, Waldy; Forsayeth, John; Cheng, Seng H; Bankiewicz, Krystof S; Shihabuddin, Lamya S

Distribution of nanoparticles throughout the cerebral cortex of rodents and non-human primates: Implications for gene and drug therapy

纳米颗粒在啮齿动物和非人灵长类动物大脑皮层的分布:对基因和药物治疗的启示

Salegio, Ernesto A; Streeter, Hillary; Dube, Nikhil; Hadaczek, Piotr; Samaranch, Lluis; Kells, Adrian P; San Sebastian, Waldy; Zhai, Yuying; Bringas, John; Xu, Ting; Forsayeth, John; Bankiewicz, Krystof S

Cerebral infusion of AAV9 vector-encoding non-self proteins can elicit cell-mediated immune responses.

将编码非自身蛋白的 AAV9 载体注入大脑可以引发细胞介导的免疫反应

Ciesielska Agnieszka, Hadaczek Piotr, Mittermeyer Gabriele, Zhou Shangzhen, Wright J Fraser, Bankiewicz Krystof S, Forsayeth John

Anterograde axonal transport of AAV2-GDNF in rat basal ganglia

大鼠基底神经节中AAV2-GDNF的前向轴突运输

Ciesielska, Agnieszka; Mittermeyer, Gabriele; Hadaczek, Piotr; Kells, Adrian P; Forsayeth, John; Bankiewicz, Krystof S

Regeneration of the MPTP-lesioned dopaminergic system after convection-enhanced delivery of AAV2-GDNF.

通过对流增强递送 AAV2-GDNF 可促进 MPTP 损伤的多巴胺能系统的再生

Kells Adrian P, Eberling Jamie, Su Xiaomin, Pivirotto Philip, Bringas John, Hadaczek Piotr, Narrow Wade C, Bowers William J, Federoff Howard J, Forsayeth John, Bankiewicz Krystof S

Real-time MR imaging of adeno-associated viral vector delivery to the primate brain

利用实时磁共振成像技术观察腺相关病毒载体递送至灵长类动物脑部的过程

Fiandaca, Massimo S; Varenika, Vanja; Eberling, Jamie; McKnight, Tracy; Bringas, John; Pivirotto, Phillip; Beyer, Janine; Hadaczek, Piotr; Bowers, William; Park, John; Federoff, Howard; Forsayeth, John; Bankiewicz, Krystof S