Protocol for NAC Attack, a phase-3, multicenter randomized, parallel, double masked, placebo controlled trial evaluating the efficacy and safety of oral N-acetylcysteine (NAC) in patients with retinitis pigmentosa
NAC Attack方案是一项3期、多中心、随机、平行、双盲、安慰剂对照试验,旨在评估口服N-乙酰半胱氨酸(NAC)治疗视网膜色素变性患者的疗效和安全性。
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doi:10.1101/2025.11.05.25339486
Kong, Xiangrong; Ibukun, Folahan; Khan, Muhammad J; Hafiz, Gulnar; Wehling, Dagmar; Dreger, Kurt; Singh, Mandeep; Birch, David; Jaffe, Glenn; Naufal, Fahd; Traboulsi, Elias I; Duncan, Jacque; Hufnagel, Rob; Carroll, Joseph; Lu, Yuchen; Matsui, Rodrigo; Moulton, Lawrence H; Hawkins, Barbara; Campochiaro, Peter A