Targeted Proteomics upon Treatment with Tofersen Identifies Novel Response Markers for Superoxide Dismutase 1-Linked Amyotrophic Lateral Sclerosis
托弗森治疗后的靶向蛋白质组学鉴定出超氧化物歧化酶 1 相关肌萎缩侧索硬化症的新型反应标志物
期刊:Annals of Neurology
影响因子:7.7
doi:10.1002/ana.70025
Steffke, Christina; Baskar, Karthik; Bachhuber, Franziska; Wiesenfarth, Maximilian; Dorst, Johannes; Schuster, Joachim; Schöberl, Florian; Reilich, Peter; Regensburger, Martin; German, Alexander; Günther, René; Vidovic, Maximilian; Petri, Susanne; Meyer, Thomas; Hagenacker, Tim; Grosskreutz, Julian; Weyen, Ute; Weydt, Patrick; Haarmeier, Thomas; Lingor, Paul; Wolf, Joachim; Hermann, Andreas; Prudlo, Johannes; Günther, Kornelia; Knehr, Antje; Elmas, Zeynep; Uzelac, Zeljko; Witzel, Simon; Ruf, Wolfgang Philipp; Freischmidt, Axel; Ho, Ritchie; Ludolph, Albert C; Weishaupt, Jochen H; Tumani, Hayrettin; Oeckl, Patrick; Brenner, David; Catanese, Alberto