Observational study of spinal muscular atrophy type 2 and 3: functional outcomes over 1 year
脊髓性肌萎缩症2型和3型的观察性研究:1年功能结局
期刊:
影响因子:
doi:10.1001/archneurol.2010.373
Kaufmann, Petra; McDermott, Michael P; Darras, Basil T; Finkel, Richard; Kang, Peter; Oskoui, Maryam; Constantinescu, Andrei; Sproule, Douglas Michael; Foley, A Reghan; Yang, Michele; Tawil, Rabi; Chung, Wendy; Martens, Bill; Montes, Jacqueline; O'Hagen, Jessica; Dunaway, Sally; Flickinger, Jean M; Quigley, Janet; Riley, Susan; Glanzman, Allan M; Benton, Maryjane; Ryan, Patricia A; Irvine, Carrie; Annis, Christine L; Butler, Hailly; Caracciolo, Jayson; Montgomery, Megan; Marra, Jonathan; Koo, Benjamin; De Vivo, Darryl C