Restoration of dystrophin expression in mice by suppressing a nonsense mutation through the incorporation of unnatural amino acids
通过加入非天然氨基酸抑制无义突变,恢复小鼠肌营养不良蛋白的表达
期刊:Nature Biomedical Engineering
影响因子:26.8
doi:10.1038/s41551-021-00774-1
Ningning Shi #, Qi Yang #, Haoran Zhang #, Jiaqi Lu, Haishuang Lin, Xu Yang, Aikedan Abulimiti, Jialu Cheng, Yu Wang, Le Tong, Tianchang Wang, Xiaodong Zhang, Hongmin Chen, Qing Xia