日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Application of in-vitro-cultured primary hepatocytes to evaluate species translatability and AAV transduction mechanisms of action.

应用体外培养的原代肝细胞评估物种转化性和 AAV 转导作用机制

Liu Su, Razon Lisa, Ritchie Olivia, Sihn Choong-Ryoul, Handyside Britta, Berguig Geoffrey, Woloszynek Jill, Zhang Lening, Batty Paul, Lillicrap David, Agrawal Vishal, Cortesio Christa, Gebretsadik Kahsay, Akeefe Hassibullah, Colosi Peter, Kim Benjamin, Bunting Stuart, Fong Sylvia

Induction of ER Stress by an AAV5 BDD FVIII Construct Is Dependent on the Strength of the Hepatic-Specific Promoter.

AAV5 BDD FVIII 构建体诱导内质网应激取决于肝脏特异性启动子的强度

Fong Sylvia, Handyside Britta, Sihn Choong-Ryoul, Liu Su, Zhang Lening, Xie Lin, Murphy Ryan, Galicia Nicole, Yates Bridget, Minto Wesley C, Vitelli Catherine, Harmon Danielle, Ru Yuanbin, Yu Guoying Karen, Escher Claudia, Vowinckel Jakob, Woloszynek Jill, Akeefe Hassib, Mahimkar Rajeev, Bullens Sherry, Bunting Stuart

Correction: Intermittent enzyme replacement therapy prevents Neu1 deficiency

更正:间歇性酶替代疗法可预防Neu1缺乏症

Luu, Amanda R; Wong, Cara; Agrawal, Vishal; Wise, Nathan; Handyside, Britta; Lo, Melanie J; Pacheco, Glenn; Felix, Jessica B; Giaramita, Alexander; d'Azzo, Alessandra; Vincelette, Jon; Bullens, Sherry; Bunting, Stuart; Christianson, Terri M; Hague, Charles M; LeBowitz, Jonathan H; Yogalingam, Gouri