Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis
化学修饰的 hCFTR mRNA 可恢复囊性纤维化小鼠模型中的肺功能
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-018-34960-0
A K M Ashiqul Haque, Alexander Dewerth, Justin S Antony, Joachim Riethmüller, Georg R Schweizer, Petra Weinmann, Ngadhnjim Latifi, Hanzey Yasar, Nicoletta Pedemonte, Elvira Sondo, Brian Weidensee, Anjali Ralhan, Julie Laval, Patrick Schlegel, Christian Seitz, Brigitta Loretz, Claus-Michael Lehr, Rup