日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Optimized chemical structure extends silencing duration of therapeutic siRNAs in dividing cancer and immune cells

优化的化学结构延长了治疗性siRNA在分裂的癌细胞和免疫细胞中的沉默持续时间。

Kremer, Anastasia; Ryaykenen, Tatyana; Segarra-Visent, Xavier; Sauer, Melanie; Breuer, Leon; Wu, Yiying; Tang, Qi; Cooper, David A; Echeverria, Dimas; Philouze, Clothilde; Bayon, Emilie; Georgess, Dan; Haraszti, Reka A

RNA Therapeutics for Improving CAR T-cell Safety and Efficacy

RNA疗法在提高CAR-T细胞疗法的安全性和有效性方面的应用

Schaible, Philipp; Bethge, Wolfgang; Lengerke, Claudia; Haraszti, Reka Agnes

Chimeric miRNA cluster enables multiplex and titratable gene inhibition in CAR-T cells

嵌合 miRNA 簇可在 CAR-T 细胞中实现多重和可滴定基因抑制

Haraszti, Reka Agnes

Comparative route of administration studies using therapeutic siRNAs show widespread gene modulation in Dorset sheep

利用治疗性siRNA进行的给药途径比较研究表明,多塞特绵羊体内存在广泛的基因调控。

Ferguson, Chantal M; Godinho, Bruno Mdc; Alterman, Julia F; Coles, Andrew H; Hassler, Matthew; Echeverria, Dimas; Gilbert, James W; Knox, Emily G; Caiazzi, Jillian; Haraszti, Reka A; King, Robert M; Taghian, Toloo; Puri, Ajit; Moser, Richard P; Gounis, Matthew J; Aronin, Neil; Gray-Edwards, Heather; Khvorova, Anastasia

Diverse lipid conjugates for functional extra-hepatic siRNA delivery in vivo.

用于体内功能性肝外siRNA递送的多种脂质缀合物

Biscans Annabelle, Coles Andrew, Haraszti Reka, Echeverria Dimas, Hassler Matthew, Osborn Maire, Khvorova Anastasia

Serum Deprivation of Mesenchymal Stem Cells Improves Exosome Activity and Alters Lipid and Protein Composition

血清剥夺可改善间充质干细胞的外泌体活性并改变其脂质和蛋白质组成。

Haraszti, Reka Agnes; Miller, Rachael; Dubuke, Michelle L; Rockwell, Hannah E; Coles, Andrew H; Sapp, Ellen; Didiot, Marie-Cecile; Echeverria, Dimas; Stoppato, Matteo; Sere, Yves Y; Leszyk, John; Alterman, Julia F; Godinho, Bruno M D C; Hassler, Matthew R; McDaniel, Justice; Narain, Niven R; Wollacott, Rachel; Wang, Yang; Shaffer, Scott A; Kiebish, Michael A; DiFiglia, Marian; Aronin, Neil; Khvorova, Anastasia

Extracellular vesicles from mice with alcoholic liver disease carry a distinct protein cargo and induce macrophage activation through heat shock protein 90

患有酒精性肝病的小鼠的细胞外囊泡携带独特的蛋白质货物,并通过热休克蛋白90诱导巨噬细胞活化。

Saha, Banishree; Momen-Heravi, Fatemeh; Furi, Istvan; Kodys, Karen; Catalano, Donna; Gangopadhyay, Anwesha; Haraszti, Reka; Satishchandran, Abhishek; Iracheta-Vellve, Arvin; Adejumo, Adeyinka; Shaffer, Scott A; Szabo, Gyongyi

Chitosan-Mangafodipir nanoparticles designed for intranasal delivery of siRNA and DNA to brain

壳聚糖-锰磷酸二氢钠纳米颗粒设计用于经鼻腔递送siRNA和DNA至大脑

Sanchez-Ramos, Juan; Song, Shijie; Kong, Xiaoyuan; Foroutan, Parastou; Martinez, Gary; Dominguez-Viqueria, William; Mohapatra, Shyam; Mohapatra, Subhra; Haraszti, Reka A; Khvorova, Anastasia; Aronin, Neil; Sava, Vasyl

5΄-Vinylphosphonate improves tissue accumulation and efficacy of conjugated siRNAs in vivo.

5α-乙烯基膦酸酯可提高结合型siRNA在体内的组织积累和疗效

Haraszti Reka A, Roux Loic, Coles Andrew H, Turanov Anton A, Alterman Julia F, Echeverria Dimas, Godinho Bruno M D C, Aronin Neil, Khvorova Anastasia

Synthesis and Evaluation of Parenchymal Retention and Efficacy of a Metabolically Stable O-Phosphocholine-N-docosahexaenoyl-l-serine siRNA Conjugate in Mouse Brain.

合成和评价代谢稳定的 O-磷酸胆碱-N-二十二碳六烯酰-L-丝氨酸 siRNA 缀合物在小鼠脑中的实质保留和功效

Nikan Mehran, Osborn Maire F, Coles Andrew H, Biscans Annabelle, Godinho Bruno M D C, Haraszti Reka A, Sapp Ellen, Echeverria Dimas, DiFiglia Marian, Aronin Neil, Khvorova Anastasia