Rescue of lysosomal acid lipase deficiency in mice by rAAV8 liver gene transfer.
利用 rAAV8 肝脏基因转移挽救小鼠溶酶体酸性脂肪酶缺乏症
期刊:Commun Med (Lond)
影响因子:
doi:10.1038/s43856-025-00816-8
Laurent Marine, Harb Rim, Jenny Christine, Oustelandt Julie, Jimenez Simon, Cosette Jeremie, Landini Francesca, Ferrante Aristide, Corre Guillaume, Vujic Nemanja, Piccoli Claudia, Brassier Anais, Van Wittenberghe Laetitia, Ronzitti Giuseppe, Kratky Dagmar, Pacelli Consiglia, Amendola Mario
