Modification of the VP1u region boosts transduction of adeno-associated virus vectors for ocular gene therapy.
VP1u 区域的修饰可增强腺相关病毒载体在眼部基因治疗中的转导。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2026.01.029
Cui Mengtian, Cheng Shun-Yun, Liang Jialing, McGowan Jackson, Xu Meiyu, Xu Guangchao, Luo Li, Wu Joae, Harman Christine D, Jacobson Amanda L, Kapeller Lydia E, Mayes Melaney A, Namkung Suk, Sharma Tapan, Leland Thomas B, Zhang Fang, Yip Mitchell, Rossmiller Brian, Xue Thomas, Chen Xiupeng, Boonying Wassamon, Lotun Anoushka, Wang Dan, Su Qin, Xie Jun, Wei Yuquan, Rothstein Ann M, Gregory-Ksander Meredith S, Komaromy Andras, Tian Bo, Lin Haijiang, Punzo Claudio, Tai Phillip W L, Gao Guangping