Comparison of Model-Predicted and Observed Evinacumab Pharmacokinetics and Efficacy in Children Aged < 5 Years With Homozygous Familial Hypercholesterolemia
比较模型预测和观察到的 Evinacumab 在 5 岁以下纯合子家族性高胆固醇血症患儿中的药代动力学和疗效
期刊:Cpt-Pharmacometrics & Systems Pharmacology
影响因子:3
doi:10.1002/psp4.70017
Bihorel, Sébastien; Dingman, Robert; Mendell, Jeanne; Norman, Katy C; George, Richard T; Zhao, Xue-Qiao; Pordy, Robert; Garcia, Daniel; Putnam, Wendy S; Raghuveer, Geetha; McCrindle, Brian W; Fornari, Elena; Baric, Ivo; Srinivasan, Shubha; Diamond, Melissa; Brinton, Eliot A; Davis, John D; DiCioccio, A Thomas; Harnisch, Lutz