日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Oral splicing modulator branaplam in Huntington's disease: a phase 2 randomized controlled trial

口服剪接调节剂布拉那普拉姆治疗亨廷顿病:一项 II 期随机对照试验

Borowsky, Beth; Ramos, Harry; Caputo, Angelika; Hartmann, Andreas; Faller, Thomas; Peters, Thomas; Sui, Yihan; Liu, Fonda; Meadowcroft, Mark; David, Olivier J; Laisney, Marc; Kinhikar, Arvind; Marder, Karen S; Tabrizi, Sarah J; Landwehrmeyer, G Bernhard; Leavitt, Blair R

Pivekimab Sunirine in Blastic Plasmacytoid Dendritic Cell Neoplasm

Pivekimab Sunirine 治疗浆细胞样树突状细胞肿瘤

Pemmaraju, Naveen; Marconi, Giovanni; Montesinos, Pau; Lane, Andrew A; Mazzarella, Luca; Sallman, David A; Ulrickson, Matthew L; Schiller, Gary J; Erba, Harry P; Wang, Eunice S; Walter, Roland B; Deconinck, Eric; Aribi, Ahmed; Legrand, Ollivier; Lebon, Delphine; Maisano, Valerio; Martinelli, Giovanni; DeAngelo, Daniel J; Derenzini, Enrico; Du, Yining; Lakshmikanthan, Sribalaji; Potluri, Jalaja; Kantarjian, Hagop M; Daver, Naval G

Prospective Validation of Circulating Tumor DNA Measurable Residual Disease After First-Line Therapy in Large B-Cell Lymphoma

一线治疗后大B细胞淋巴瘤循环肿瘤DNA可测量残留病灶的前瞻性验证

Wang, Steven; Nijland, Marcel; Strobbe, Leonie; Oosterveld, Margriet; Boersma, Rinske; Koene, Harry; Klerk, Clara; de Jongh, Eva; Koster, Ad; Pruijt, Hans; van der Poel, Marjolein; van Werkhoven, Erik; Zanders, Helma; Dinmohamed, Avinash; Pegtel, Michiel; Meek, Stephanie; Stowell, Sierra Love; Warinske, Hayley; Alizadeh, Ash A; Kurtz, David M; Chamuleau, Martine E D

The TransEuro open-label trial of human fetal ventral mesencephalic transplantation in patients with moderate Parkinson's disease

TransEuro 是一项开放标签试验,旨在研究人类胎儿腹侧中脑移植治疗中度帕金森病患者的疗效。

Barker, Roger A; Lao-Kaim, Nicholas P; Guzman, Natalie Valle; Athauda, Dilan; Bjartmarz, Hjalmar; Björklund, Anders; Church, Alistair; Cutting, Emma; Daft, Danielle; Dayal, Viswas; Dunnett, Stephen; Evans, Amy; Grealish, Shane; Hannaway, Naomi; He, Xiaoling; Hewitt, Sam; Kefalopoulou, Zinovia; Mahlknecht, Philipp; Martín-Bastida, Antonio; Farrell, Krista; Moore, Sarah; Bulstrode, Harry; Nakornchai, Tagore; Nelander-Wahlestedt, Jenny; Roupé, Linnea; Paul, Gesine; Peall, Kathryn; Rosser, Anne; Roca-Fernández, Adriana; Rowlands, Sophie; McGorrian, Anne-Marie; Scherf, Caroline; Vinh, Ngoc Nga; Roberton, Victoria; Kelly, Claire; Lelos, Mariah; Torres, Eduardo; Shires, Kate; Hills, Rachel; Williams, Debbie; Roussakis, Andreas-Antonios; Sibley, Krista; Tyers, Pamela; Wijeyekoon, Ruwani; Williams-Gray, Caroline; Foltynie, Thomas; Piccini, Paola; Morris, Robert; Lazic, Stanley E; Lindvall, Olle; Parmar, Malin; Widner, Hakan

Genomic and transcriptomic analyses of aortic stenosis enhance therapeutic target discovery and disease prediction.

主动脉狭窄的基因组学和转录组学分析有助于发现治疗靶点和预测疾病。

Small Aeron M, Yang Ta-Yu, Itoh Shinsuke, Thériault Sébastien, Dufresne Line, Kurosawa Ryo, Komuro Issei, Matsuda Koichi, Vy Ha My T, Farber-Eger Eric H, Shaffer Lauren Lee, Boulier Kristin M, Corey Kristin M, Ramaker Megan E, Laporte Fabien, Schott Jean-Jacques, Le Scouarnec Solena, Singh Sasha A, Sonawane Abhijeet R, Smith Harry A, Rafaels Nicholas, Ghouse Jonas, Raja Anna A, Ostrowski Sisse R, Sørensen Erik, Mikkelsen Christina, Pedersen Ole B, Erikstrup Christian, Ullum Henrik, Sveinbjornsson Gardar, Gudbjartsson Daniel F, Abner Erik, Lee Jiwoo, Ganna Andrea, Nowak-Göttl Ulrike, Finer Sarah, Schumacher Johannes, Maj Carlo, Al-Kassou Baravan, Nickenig Georg, Trenkwalder Teresa, Dreβen Martina, Krane Markus, Nöthen Markus M, Moksnes Marta R, Brumpton Ben M, Knight Stacey, Knowlton Kirk U, Nadauld Lincoln, Debiec Radek, Musameh Muntaser D, Braund Peter S, Nelson Christopher P, Czuba Tomasz, Melander Olle, Selvaraj Margaret Sunitha, Koyama Satoshi, Bhukar Rohan, Ruan Yunfeng, Ljungberg Johan, Damrauer Scott M, Levin Michael G, Franke Andre, Berger Klaus, Ruff Christian T, Melloni Giorgio E M, Kamanu Frederick K, Ito Kaoru, Do Ron, Loos Ruth J F, Schunkert Heribert, Wells Quinn S, Shah Svati H, Le Tourneau Thierry, Messika-Zeitoun David, Gignoux Christopher, Bundgaard Henning, Larsson Susanna C, Michaëlsson Karl, Holm Hilma, Helgadottir Anna, Esko Tonu, van Heel David A, Mathieu Patrick, Samani Nilesh J, Smith J Gustav, Söderberg Stefan, Rader Daniel J, Marston Nicholas A, Sabatine Marc S, Pasaniuc Bogdan, Cho Kelly, Wilson Peter W F, O'Donnell Christopher J, Stefansson Kari, Bossé Yohan, Aikawa Elena, Engert James C, Peloso Gina M, Natarajan Pradeep, Thanassoulis George

Faecalibacterium prausnitzii Induces an Anti-inflammatory Response and a Metabolic Reprogramming in Human Monocytes.

普氏粪杆菌可诱导人类单核细胞产生抗炎反应和代谢重编程。

Danne Camille, de Oliveira Formiga Rodrigo, Creusot Laura, Marquet Florian, Sedda Delphine, Hua Laura, Ruffié Pauline, Pham Hang-Phuong, Brot Loic, Alonso Salgueiro Iria, Michel Marie-Laure, Langella Philippe, Lefevre Jérémie H, Sokol Harry, Rolhion Nathalie

Postmarket Drug Safety-Related Actions Before and After the US Food and Drug Administration Amendments Act

美国食品药品监督管理局修正案颁布前后的上市后药品安全相关行动

Doernberg, Harry; Wallach, Joshua D; Jeffery, Molly M; Mooghali, Maryam; Ramachandran, Reshma; Ross, Joseph S

Mirtazapine for Methamphetamine Use Disorder: A Randomized Clinical Trial

米氮平治疗甲基苯丙胺使用障碍:一项随机临床试验

McKetin, Rebecca; Shoptaw, Steven; Saunders, Lucy; Nguyen, Long; Clare, Philip J; Dore, Gregory J; Turner, Alyna; Dean, Olivia M; Kelly, Peter J; Arunogiri, Shalini; Koeijers, Juanita; Degan, Tayla J; Degenhardt, Louisa; Farrell, Michael; Goodman-Meza, David; Sinclair, Barbara; Reid, David; Cordaro, Frank; Hill, Harry; Lundin, Robert; Hayllar, Jeremy; Christmass, Michael; Liaw, Willy; Liu, Danica; Woods, Amelia; Brewerton, Blaire; Holyoak, Ellie; Wu, Brian Tid-Fung; Maher, Hayley; O'Dea, Noni; Keygan, Joel; Kontogiannis, Ava; Palmer, Lily; Morrison, Caity; Wrobel, Anna; Hyland, Bec; Kiden, Gift; Romeo, Vanessa; Kyaw, Khine Wut Yee; Byrne, Marianne; Colledge-Frisby, Samantha; Zahra, Emma; Berk, Michael

Defective DNA Damage Response is a Targetable Therapeutic Vulnerability in ESR1 Mutant Breast Cancer.

DNA损伤反应缺陷是ESR1突变型乳腺癌的一个可靶向治疗弱点。

Herzog Sarah K, Stevens Jessica H, Gu Guowei, Grimm Sandra L, Cardoza Kloma, Hawkins Autumn G M, Lin Hangqing, Ramos Daniela, Beyer Amanda R, Edwards David G, Dustin Derek, Yang Harry J, Liang Nicole, Khan Ashfia F, Bawa-Khalfe Tasneem, McGrail Daniel J, Lin Shiaw-Yih, Coarfa Cristian, Fuqua Suzanne A W

EGFR inhibitor-resistant lung cancers exhibit collateral sensitivity to a covalent, cysteine-independent KEAP1 oligomerizing molecular bridge.

对 EGFR 抑制剂耐药的肺癌表现出对共价、不依赖半胱氨酸的 KEAP1 寡聚化分子桥的协同敏感性。

Bassil Christopher F, Dillon Kerry, Anderson Gray R, Mayro Benjamin, Askin Kayleigh N, Winter Peter S, Harry Stefan, Gruber Samuel, Hall Tierney M, Hoj Jacob P, Cerda-Smith Christian, Hutchinson Haley M, Killarney Shane T, Heffernan Ava, Teddy Caroline, Singleton Katherine R, Qin Li, Jubien-Girard Kévin, Favreau Cécile, Robert Guillaume, Tivon Barr, Livnah Ella, London Nir, Benhida Rachid, Auberger Patrick, Pendergast Ann Marie, Bar-Peled Liron, Lonard David M, Martin Anthony R, Puissant Alexandre, Wood Kris C