日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Gene Editing Rescues In vitro T Cell Development of RAG2-Deficient Induced Pluripotent Stem Cells in an Artificial Thymic Organoid System

基因编辑在人工胸腺类器官系统中挽救了 RAG2 缺陷型诱导多能干细胞的体外 T 细胞发育

Cameron L Gardner #, Mara Pavel-Dinu #, Kerry Dobbs, Marita Bosticardo, Paul K Reardon, Justin Lack, Suk See DeRavin, Kent Le, Ezekiel Bello, Francesca Pala, Ottavia M Delmonte, Harry Malech, Amelie Montel-Hagan, Gay Crooks, Oreste Acuto, Matthew H Porteus, Luigi D Notarangelo

Gene correction for SCID-X1 in long-term hematopoietic stem cells

长期造血干细胞中 SCID-X1 的基因校正

Mara Pavel-Dinu, Volker Wiebking, Beruh T Dejene, Waracharee Srifa, Sruthi Mantri, Carmencita E Nicolas, Ciaran Lee, Gang Bao, Eric J Kildebeck, Niraj Punjya, Camille Sindhu, Matthew A Inlay, Nivedita Saxena, Suk See DeRavin, Harry Malech, Maria Grazia Roncarolo, Kenneth I Weinberg, Matthew H Porteu

Recombinant Pregnancy-Specific Glycoprotein 1 Has a Protective Role in a Murine Model of Acute Graft-versus-Host Disease

重组妊娠特异性糖蛋白 1 在小鼠急性移植物抗宿主病模型中具有保护作用

Karlie Jones, Sarah Bryant, Jian Luo, Patricia Kiesler, Sherry Koontz, James Warren, Harry Malech, Elizabeth Kang, Gabriela Dveksler

PSG9 Stimulates Increase in FoxP3+ Regulatory T-Cells through the TGF-β1 Pathway

PSG9 通过 TGF-β1 通路刺激 FoxP3+ 调节性 T 细胞增加

Karlie Jones, Angela Ballesteros, Margaret Mentink-Kane, James Warren, Shemona Rattila, Harry Malech, Elizabeth Kang, Gabriela Dveksler

Expansion of immunoglobulin-secreting cells and defects in B cell tolerance in Rag-dependent immunodeficiency

Rag 依赖性免疫缺陷中免疫球蛋白分泌细胞的扩增和 B 细胞耐受性的缺陷

Jolan E Walter, Francesca Rucci, Laura Patrizi, Mike Recher, Stephan Regenass, Tiziana Paganini, Marton Keszei, Itai Pessach, Philipp A Lang, Pietro Luigi Poliani, Silvia Giliani, Waleed Al-Herz, Morton J Cowan, Jennifer M Puck, Jack Bleesing, Tim Niehues, Catharina Schuetz, Harry Malech, Suk See De