日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis

为首次在囊性纤维化患者中开展慢病毒人体试验做准备

Alton, Eric W F W; Beekman, Jeffery M; Boyd, A Christopher; Brand, June; Carlon, Marianne S; Connolly, Mary M; Chan, Mario; Conlon, Sinead; Davidson, Heather E; Davies, Jane C; Davies, Lee A; Dekkers, Johanna F; Doherty, Ann; Gea-Sorli, Sabrina; Gill, Deborah R; Griesenbach, Uta; Hasegawa, Mamoru; Higgins, Tracy E; Hironaka, Takashi; Hyndman, Laura; McLachlan, Gerry; Inoue, Makoto; Hyde, Stephen C; Innes, J Alastair; Maher, Toby M; Moran, Caroline; Meng, Cuixiang; Paul-Smith, Michael C; Pringle, Ian A; Pytel, Kamila M; Rodriguez-Martinez, Andrea; Schmidt, Alexander C; Stevenson, Barbara J; Sumner-Jones, Stephanie G; Toshner, Richard; Tsugumine, Shu; Wasowicz, Marguerite W; Zhu, Jie

Brief report: isogenic induced pluripotent stem cell lines from an adult with mosaic down syndrome model accelerated neuronal ageing and neurodegeneration

简报:来自嵌合型唐氏综合征成人模型的同源诱导多能干细胞系加速神经元衰老和神经退行性变

Murray, Aoife; Letourneau, Audrey; Canzonetta, Claudia; Stathaki, Elisavet; Gimelli, Stefania; Sloan-Bena, Frederique; Abrehart, Robert; Goh, Pollyanna; Lim, Shuhui; Baldo, Chiara; Dagna-Bricarelli, Franca; Hannan, Saad; Mortensen, Martin; Ballard, David; Syndercombe Court, Denise; Fusaki, Noemi; Hasegawa, Mamoru; Smart, Trevor G; Bishop, Cleo; Antonarakis, Stylianos E; Groet, Jürgen; Nizetic, Dean

Non-transmissible Sendai virus vector encoding c-myc suppressor FBP-interacting repressor for cancer therapy

用于癌症治疗的非传染性仙台病毒载体,编码c-myc抑制因子FBP相互作用阻遏蛋白

Matsushita, Kazuyuki; Shimada, Hideaki; Ueda, Yasuji; Inoue, Makoto; Hasegawa, Mamoru; Tomonaga, Takeshi; Matsubara, Hisahiro; Nomura, Fumio

Bi-HAC vector system toward gene and cell therapy

用于基因和细胞治疗的Bi-HAC载体系统

Iida, Yuichi; Kazuki, Yasuhiro; Hayashi, Masahiro; Ueda, Yasuji; Hasegawa, Mamoru; Kouprina, Natalay; Larionov, Vladimir; Oshimura, Mitsuo

DVC1-0101 to treat peripheral arterial disease: a Phase I/IIa open-label dose-escalation clinical trial.

DVC1-0101 治疗外周动脉疾病:一项 I/IIa 期开放标签剂量递增临床试验

Yonemitsu Yoshikazu, Matsumoto Takuya, Itoh Hiroyuki, Okazaki Jin, Uchiyama Makiko, Yoshida Kumi, Onimaru Mitsuho, Onohara Toshihiro, Inoguchi Hiroyuki, Kyuragi Ryoichi, Shimokawa Mototsugu, Ban Hiroshi, Tanaka Michiko, Inoue Makoto, Shu Tsugumine, Hasegawa Mamoru, Nakanishi Yoichi, Maehara Yoshihiko

A novel protective MHC-I haplotype not associated with dominant Gag-specific CD8+ T-cell responses in SIVmac239 infection of Burmese rhesus macaques

在缅甸恒河猴SIVmac239感染中,一种新型的保护性MHC-I单倍型与显性Gag特异性CD8+ T细胞反应无关

Takahashi, Naofumi; Nomura, Takushi; Takahara, Yusuke; Yamamoto, Hiroyuki; Shiino, Teiichiro; Takeda, Akiko; Inoue, Makoto; Iida, Akihiro; Hara, Hiroto; Shu, Tsugumine; Hasegawa, Mamoru; Sakawaki, Hiromi; Miura, Tomoyuki; Igarashi, Tatsuhiko; Koyanagi, Yoshio; Naruse, Taeko K; Kimura, Akinori; Matano, Tetsuro

Assessment of F/HN-pseudotyped lentivirus as a clinically relevant vector for lung gene therapy

评估F/HN假型慢病毒作为肺基因治疗临床相关载体的应用

Griesenbach, Uta; Inoue, Makoto; Meng, Cuixiang; Farley, Raymond; Chan, Mario; Newman, Nikki K; Brum, Andrea; You, Jun; Kerton, Angela; Shoemark, Amelia; Boyd, A Christopher; Davies, Jane C; Higgins, Tracy E; Gill, Deborah R; Hyde, Stephen C; Innes, J Alastair; Porteous, David J; Hasegawa, Mamoru; Alton, Eric W F W

Differentiation of Mouse Pancreatic Stem Cells Into Insulin-Producing Cells by Recombinant Sendai Virus-Mediated Gene Transfer Technology

利用重组仙台病毒介导的基因转移技术将小鼠胰腺干细胞分化为胰岛素分泌细胞

Yukawa, Hiroshi; Noguchi, Hirofumi; Oishi, Koichi; Miyamoto, Yoshitaka; Inoue, Makoto; Hasegawa, Mamoru; Hayashi, Shuji; Baba, Yoshinobu

Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells

诱导多能干细胞中α1-抗胰蛋白酶缺乏症的靶向基因矫正

Yusa, Kosuke; Rashid, S Tamir; Strick-Marchand, Helene; Varela, Ignacio; Liu, Pei-Qi; Paschon, David E; Miranda, Elena; Ordóñez, Adriana; Hannan, Nicholas R F; Rouhani, Foad J; Darche, Sylvie; Alexander, Graeme; Marciniak, Stefan J; Fusaki, Noemi; Hasegawa, Mamoru; Holmes, Michael C; Di Santo, James P; Lomas, David A; Bradley, Allan; Vallier, Ludovic

Synergistic effect of non-transmissible Sendai virus vector encoding the c-myc suppressor FUSE-binding protein-interacting repressor plus cisplatin in the treatment of malignant pleural mesothelioma

编码c-myc抑制因子FUSE结合蛋白相互作用阻遏物的非传染性仙台病毒载体联合顺铂治疗恶性胸膜间皮瘤的协同作用

Kitamura, Atsushi; Matsushita, Kazuyuki; Takiguchi, Yuichi; Shimada, Hideaki; Tada, Yuji; Yamanaka, Makako; Hiroshima, Kenzo; Tagawa, Masatoshi; Tomonaga, Takeshi; Matsubara, Hisahiro; Inoue, Makoto; Hasegawa, Mamoru; Sato, Yasunori; Levens, David; Tatsumi, Koichiro; Nomura, Fumio