日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Characterization of patient-derived site-specific in vivo models of pediatric-type diffuse high-grade glioma using magnetic resonance imaging

利用磁共振成像技术对儿童型弥漫性高级别胶质瘤的患者来源的部位特异性体内模型进行表征

Boult, Jessica K R; Carvalho, Diana M; Kessler, Ketty; Molinari, Valeria; Mackay, Alan; Grabovska, Yura; Fofana, Mariama; Taylor, Kathryn R; Bjerke, Lynn; Fernandez, Elisabet; Pereira, Rita; Clarke, Matthew; Temelso, Sara; Burford, Anna; Sejdiu, Drenusha; Carcaboso, Angel M; Cockle, Julia V; Carceller, Fernando; Marshall, Lynley V; Vaidya, Sucheta J; Bridges, Leslie R; Singh, Navneet; Stapleton, Simon; Hettige, Samantha; Al-Sarraj, Safa; Reisz, Zita; Zebian, Bassel; Bleil, Cristina; Grundy, Richard G; Gray, Juliet C; Hargrave, Darren; Wilson, Shaun; Picton, Susan; Adamski, Jenny K; Hassall, Timothy E G; Mastronuzzi, Angela; Carai, Andrea; Benjamin, Philip; Colafati, G Stefania; Vinci, Maria; Jones, Chris; Robinson, Simon P

Author Correction: The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

作者更正:II型RAF抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II期FIREFLY-1试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

II 型 RAF 抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II 期 FIREFLY-1 试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

High-grade glioma in infants and young children is histologically, molecularly, and clinically diverse: Results from the SJYC07 trial and institutional experience

婴幼儿高级别胶质瘤在组织学、分子生物学和临床表现上具有多样性:来自 SJYC07 试验和机构经验的结果

Chiang, Jason; Bagchi, Aditi; Li, Xiaoyu; Dhanda, Sandeep K; Huang, Jie; Pinto, Soniya N; Sioson, Edgar; Dalton, James; Tatevossian, Ruth G; Jia, Sujuan; Partap, Sonia; Fisher, Paul G; Bowers, Daniel C; Hassall, Timothy E G; Lu, Congyu; Zaldivar-Peraza, Airen; Wright, Karen D; Broniscer, Alberto; Qaddoumi, Ibrahim; Upadhyaya, Santhosh A; Vinitsky, Anna; Sabin, Noah D; Orr, Brent A; Klimo, Paul Jr; Boop, Frederick A; Ashford, Jason M; Conklin, Heather M; Onar-Thomas, Arzu; Zhou, Xin; Ellison, David W; Gajjar, Amar; Robinson, Giles W

CTNI-09. TYPE II RAF INHIBITOR TOVORAFENIB IN RELAPSED/REFRACTORY (R/R) PEDIATRIC LOW-GRADE GLIOMA (PLGG): RESULTS FROM PATIENTS ON A DRUG HOLIDAY (DH) IN THE PHASE 2 FIREFLY-1 TRIAL

CTNI-09. II型RAF抑制剂托沃拉非尼治疗复发/难治性(R/R)儿童低级别胶质瘤(PLGG):FIREFLY-1 II期试验中停药(DH)患者的结果

Veiga, Luís D; Teixeira, Inês F; Vaz, Joana B; Leite, Paula; Gonçalves, Joana; Perreault, Sébastien; Khuong-Quang, Dong-Anh; Kilburn, Lindsay B; Landi, Daniel B; Leary, Sarah E S; Bailey, Simon; Larouche, Valérie; Nysom, Karsten; Driever, Pablo Hernáiz; Baxter, Patricia A; Witt, Olaf; Oren, Michal Yalon; Abdelbaki, Mohamed S; Kline, Cassie; Whipple, Nicholas S; Ziegler, David S; van der Lugt, Jasper; Hassall, Timothy E; Gerber, Nicolas U; Segal, Devorah; Hansford, Jordan R; McCowage, Geoffrey; Kang, Hyoung Jin; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Toledano, Helen; Jabado, Nada; Gottardo, Nicholas G; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Hoke, Molly E; Kim, Yeonhee; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Waanders, Angela J

NFS-03. MEDULLOBLASTOMA IN CHILDREN WITH FANCONI ANEMIA: ASSOCIATION WITH FA-D1/FA-N, SHH TYPE AND POOR SURVIVAL INDEPENDENT OF TREATMENT STRATEGIES

NFS-03. 范可尼贫血患儿髓母细胞瘤:与 FA-D1/FA-N、SHH 型及与治疗策略无关的低生存率相关

Chukwu, Wolu; Lee, Siyun; Crane, Alexander; Zhang, Shu; Webster, Sophie; Mittra, Ipsa; Imielinski, Marcin; Beroukhim, Rameen; Dubois, Frank; Dalin, Simona; Seelow, Dominik; Öz, Elif; Hardt, Annika; Kortmann, Rolf-Dieter; Schwarz, Rudolf; Timmermann, Beate; Bison, Brigitte; Warmuth-Metz, Monika; von Hoff, Katja; von Bueren, André O; Gerber, Nicolas U; Fleischhack, Gudrun; Pietsch, Torsten; Pfister, Stefan M; Sturm, Dominik; Mynarek, Martin; Rutkowski, Stefan; Obrecht-Sturm, Denise; Faria Andrade*, Augusto; Sigaud*, Romain; Puligandla*, Evan; Liu, Bridget; Karimi, Elham; Schmid, Simone; Selt, Florian; Driever, Pablo Hernáiz; Koch, Arend; Sahm, Felix; Sievers, Philipp; Pfister, Stefan M; Witt, Olaf; Jones, David T W; Capper, David; Walsh*, Logan; Jabado*, Nada; Milde*, Till; Ghasemi, David R; von Hoff, Katja; Obrecht-Sturm, Denise; Wenning, Janna; Mynarek, Martin; Gerber, Nicolas U; Benesch, Martin; Juhnke, Björn O; Bison, Brigitte; Warmuth-Metz, Monika; Timmermann, Beate; Faldum, Andreas; Fleischhack, Gudrun; Grotzer, Michael; Driever, Pablo Hernáiz; Beilken, Andreas; Ebinger, Martin; Graf, Norbert; Frühwald, Michael; Schmid, Irene; Koch, Arend; Bergmann, Markus; Hagel, Christian; Coras, Roland; Blümcke, Ingmar; Reifenberger, Guido; Felsberg, Jörg; Keyvani, Kathy; Harter, Patrick N; Prinz, Marco; Staszewski, Ori; Acker, Till; Brück, Wolfgang; Hartmann, Christian; von Deimling, Andreas; Sommer, Clemens; Hasselblatt, Martin; Riemenschneider, Markus J; Monoranu, Camelia-Maria; Rushing, Elisabeth; Kool, Marcel; Pfister, Stefan M; Schüller, Ulrich; Pietsch, Torsten; Kortmann, Rolf D; Kwiecien, Robert; Witt, Hendrik; Pajtler, Kristian W; Rutkowski, Stefan; Fruehwald, Michael C; Boros, Matej; Dahlum, Sonja; Bens, Susanne; Johann, Pascal D; Kachanov, Denis; Hauser, Peter; Kratz, Christian P; Hernaiz-Driever, Pablo; Eyrich, Matthias; Sumerauer, David; Milde, Till; Reinhard, Harald; van de Wetering, Marianne; Gil-da-Costa, Maria Joao; Elisabetta, Schiavello; Kerl, Kornelius; Furtwaengler, Rhoikos; Kordes, Uwe; Gerss, Joachim; Hasselblatt, Martin; Nysom, Karsten; Nemes, Karolina; Kline, Cassie; Waanders, Angela J; Ziegler, David S; Kilburn, Lindsay B; Nysom, Karsten; van der Lugt, Jasper; Hassall, Timothy E; Gerber, Nicolas U; Segal, Devorah; Larouche, Valérie; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Oren, Michal Yalon; Toledano, Helen; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Whipple, Nicholas S; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Wright, Karen D; Blackman, Samuel C; Qiu, Jiaheng; Podesta, Dolores; Walter, Ashley; Da Costa, Daniel; Manley, Peter; McLeod, Lisa; Landi, Daniel B; Geisemeyer, Neal; Federico, Aniello; Sill, Martin; Rosenblum, Marc; Bale, Tejus; Mauermann, Monika; Schrimpf, Daniel; Johann, Pascal; Pickles, Jessica; Aldape, Kenneth; Tauziède-Espariat, Arnault; Hasselblatt, Martin; Sturm, Dominik; Tietze, Anna; von Deimling, Andreas; Sievers, Philipp; Sahm, Felix; Gojo, Johannes; von Hoff, Katja; Pfister, Stefan M; Kool, Marcel; Keck, Michaela-Kristina; Tietze, Anna; Sievers, Philipp; Bison, Brigitte; Avula, Shivaram; Brandner, Sebastian; Cheesman, Edmund; Faure-Conter, Cécile; Fenouil, Tanguy; Figarella-Branger, Dominique; Gauchotte, Guillaume; Goebell, Einar; Gojo, Johannes; Haberler, Christine; Hakumäki, Juhana; Hayden, James T; Jabado, Nada; Korhonen, Laura S; Korshunov, Andrey; Koscielniak, Ewa; Kramm, Christof M; Kranendonk, Mariëtte E G; Lavarino, Cinzia; Lequin, Maarten; Loiseau, Hugues; Ludlow, Louise E; Maher, Ossama; Meyronet, David; Nyman, Per; Øra, Ingrid; Perwein, Thomas; Pesola, Jouni; Rauramaa, Tuomas; Reddingius, Roel; Samuel, David; Schouten-van Meeteren, Antoinette Y N; Schüller, Ulrich; Sexton-Oates, Alexandra; Solomon, David; Varlet, Pascale; Vasiljevic, Alexandre; von Kalle, Thekla; Wefers, Annika K; Wesseling, Pieter; White, Christine; Zamecnik, Josef; Zapotocky, Michal; von Hoff*, Katja; Jones*, David T W; Stepien, Natalia; Senfter, Daniel; Freund, Julia; Machreich, Sarah; Bruckner, Katharina; Mager, Leah; Laemmerer, Anna; Jaunecker, Carola; Pirker, Christine; Lötsch-Gojo, Daniela; Mayr, Lisa; Hedrich, Cora; Lippolis, Maria Aliotti; Schned, Hannah; Köller, Clara; Kiesel, Barbara; Dorfer, Christian; Azizi, Amedeo A; Peyrl, Andreas; Schmook, Maria T; Euskirchen, Philipp; Pagès-Gallego, Marc; Vermeulen, Carlo; Tops, Bastiaan; Haberler, Christine; Müllauer, Leonhard; Madlener, Sibylle; Gojo, Johannes; Schned, Hannah; Haberler, Christine; Peyrl, Andreas; Azizi, Amedeo; Mayr, Lisa; Aistleitner, Barbara; von Hoff, Katja; Kool, Marcel; Kjaersgaard, Mimi; Trkova, Katerina; Andre, Nicolas; Lippolis, Maria Aliotti; Hedrich, Cora; Köller, Clara; Stepien, Natalia; Slavc, Irene; Gojo, Johannes; Traunwieser, Thomas; Loos, Elena; Ottensmeier, Holger; Mynarek, Martin; Bison, Brigitte; Kandels, Daniela; Rossius, Anne; Lüttich, Peggy; Baust, Katja; Faulstich-Ritter, Kristin; John, Rainer; Kreisch, Andrea; Landmann, Judyta; Manteufel, Eva; Nest, Alexandra; Prüfe, Jenny; Schubert, Lisa; Stamm, Walther; Timmermann, Beate; Gerss, Joachim; Rutkowski, Stefan; Schlegel, Paul-Gerhardt; Eyrich, Matthias; Gnekow, Astrid K; Frühwald, Michael C; Sönksen, Marthe; Obrecht-Sturm, Denise; Driever, Pablo Hernáiz; Sauerbrey, Axel; Graf, Norbert; Kontny, Udo; Reimann, Christian; Kordes, Uwe; Schwarz, Rudolf; Obser, Tobias; Boschann, Felix; Schüller, Ulrich; Altendorf, Lea; Goschzik, Tobias; Pietsch, Torsten; Mynarek, Martin; Rutkowski, Stefan

Clinical Outcomes and Patient-Matched Molecular Composition of Relapsed Medulloblastoma

复发性髓母细胞瘤的临床结果和患者匹配的分子组成

Kumar, Rahul; Smith, Kyle S; Deng, Maximilian; Terhune, Colt; Robinson, Giles W; Orr, Brent A; Liu, Anthony P Y; Lin, Tong; Billups, Catherine A; Chintagumpala, Murali; Bowers, Daniel C; Hassall, Timothy E; Hansford, Jordan R; Khuong-Quang, Dong Anh; Crawford, John R; Bendel, Anne E; Gururangan, Sridharan; Schroeder, Kristin; Bouffet, Eric; Bartels, Ute; Fisher, Michael J; Cohn, Richard; Partap, Sonia; Kellie, Stewart J; McCowage, Geoffrey; Paulino, Arnold C; Rutkowski, Stefan; Fleischhack, Gudrun; Dhall, Girish; Klesse, Laura J; Leary, Sarah; Nazarian, Javad; Kool, Marcel; Wesseling, Pieter; Ryzhova, Marina; Zheludkova, Olga; Golanov, Andrey V; McLendon, Roger E; Packer, Roger J; Dunham, Christopher; Hukin, Juliette; Fouladi, Maryam; Faria, Claudia C; Pimentel, Jose; Walter, Andrew W; Jabado, Nada; Cho, Yoon-Jae; Perreault, Sebastien; Croul, Sidney E; Zapotocky, Michal; Hawkins, Cynthia; Tabori, Uri; Taylor, Michael D; Pfister, Stefan M; Klimo, Paul Jr; Boop, Frederick A; Ellison, David W; Merchant, Thomas E; Onar-Thomas, Arzu; Korshunov, Andrey; Jones, David T W; Gajjar, Amar; Ramaswamy, Vijay; Northcott, Paul A

Pulmonary Function After Treatment for Embryonal Brain Tumors on SJMB03 That Included Craniospinal Irradiation

SJMB03 研究中接受颅脊髓照射治疗的胚胎性脑肿瘤患者的肺功能

Green, Daniel M; Merchant, Thomas E; Billups, Catherine A; Stokes, Dennis C; Broniscer, Alberto; Bartels, Ute; Chintagumpala, Murali; Hassall, Timothy E; Gururangan, Sridharan; McCowage, Geoffrey B; Heath, John A; Cohn, Richard J; Fisher, Michael J; Srinivasan, Ashok; Robinson, Giles W; Gajjar, Amar

Results of a phase 1 study utilizing monocyte-derived dendritic cells pulsed with tumor RNA in children and young adults with brain cancer.

一项利用肿瘤 RNA 脉冲单核细胞衍生树突状细胞治疗脑癌儿童和青少年的 1 期研究结果

Caruso Denise A, Orme Lisa M, Neale Alana M, Radcliff Fiona J, Amor Gerlinda M, Maixner Wirginia, Downie Peter, Hassall Timothy E, Tang Mimi L K, Ashley David M