Application of in-vitro-cultured primary hepatocytes to evaluate species translatability and AAV transduction mechanisms of action.
应用体外培养的原代肝细胞评估物种转化性和 AAV 转导作用机制
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2022.05.008
Liu Su, Razon Lisa, Ritchie Olivia, Sihn Choong-Ryoul, Handyside Britta, Berguig Geoffrey, Woloszynek Jill, Zhang Lening, Batty Paul, Lillicrap David, Agrawal Vishal, Cortesio Christa, Gebretsadik Kahsay, Akeefe Hassibullah, Colosi Peter, Kim Benjamin, Bunting Stuart, Fong Sylvia