日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lipid nanoparticle-mediated mRNA delivery to CD34(+) cells in rhesus monkeys.

脂质纳米颗粒介导的mRNA递送至恒河猴CD34(+)细胞

Kim Hyejin, Zenhausern Ryan, Gentry Kara, Lian Liming, Huayamares Sebastian G, Radmand Afsane, Loughrey David, Podilapu Ananda R, Hatit Marine Z C, Ni Huanzhen, Li Andrea, Shajii Aram, Peck Hannah E, Han Keyi, Hua Xuanwen, Jia Shu, Martinez Michele, Lee Charles, Santangelo Philip J, Tarantal Alice, Dahlman James E

Cross‐species systems biology target prioritization leads to the development of antisense oligonucleotides as a potential therapeutic approach for progressive supranuclear palsy

跨物种系统生物学靶点优先排序促成了反义寡核苷酸作为进行性核上性麻痹潜在治疗方法的开发。

Hatit, Marine Z C; Reichenbach, Linus F; Tobin, John M; Vilela, Filipe; Burley, Glenn A; Watson, Allan J B; Min, Yuhao; Wang, Xue; Bergman, Jeremiah; Sotelo, Katie D; Reddy, Joseph S; Quicksall, Zachary; Nguyen, Thuy; Mitchell, Adriana O; Dickson, Dennis W; Kawatani, Keiji; Inoue, Yasuteru; Kanekiyo, Takahisa; Allen, Mariet; Is, Ozkan; Ertekin‐Taner, Nilüfer

Cationic cholesterol-dependent LNP delivery to lung stem cells, the liver, and heart

阳离子胆固醇依赖性 LNP 输送至肺干细胞、肝脏和心脏

Afsane Radmand, Hyejin Kim, Jared Beyersdorf, Curtis N Dobrowolski, Ryan Zenhausern, Kalina Paunovska, Sebastian G Huayamares, Xuanwen Hua, Keyi Han, David Loughrey, Marine Z C Hatit, Ada Del Cid, Huanzhen Ni, Aram Shajii, Andrea Li, Abinaya Muralidharan, Hannah E Peck, Karen E Tiegreen, Shu Jia, Ph

Nanoparticle stereochemistry-dependent endocytic processing improves in vivo mRNA delivery

纳米颗粒立体化学依赖的内吞作用可改善体内mRNA递送

Hatit, Marine Z C; Dobrowolski, Curtis N; Lokugamage, Melissa P; Loughrey, David; Ni, Huanzhen; Zurla, Chiara; Da Silva Sanchez, Alejandro J; Radmand, Afsane; Huayamares, Sebastian G; Zenhausern, Ryan; Paunovska, Kalina; Peck, Hannah E; Kim, Jinwhan; Sato, Manaka; Feldman, Jacob I; Rivera, Michael-Alexander; Cristian, Ana; Kim, YongTae; Santangelo, Philip J; Dahlman, James E

Substituting racemic ionizable lipids with stereopure ionizable lipids can increase mRNA delivery

用立体纯的电离脂质替代外消旋的电离脂质可以提高mRNA的递送效率。

Da Silva Sanchez, Alejandro J; Zhao, Kun; Huayamares, Sebastian G; Hatit, Marine Z C; Lokugamage, Melissa P; Loughrey, David; Dobrowolski, Curtis; Wang, Shuaishuai; Kim, Hyejin; Paunovska, Kalina; Kuzminich, Yanina; Dahlman, James E

The Transcriptional Response to Lung-Targeting Lipid Nanoparticles in Vivo

肺靶向脂质纳米颗粒在体内的转录反应

Radmand, Afsane; Lokugamage, Melissa P; Kim, Hyejin; Dobrowolski, Curtis; Zenhausern, Ryan; Loughrey, David; Huayamares, Sebastian G; Hatit, Marine Z C; Ni, Huanzhen; Del Cid, Ada; Da Silva Sanchez, Alejandro J; Paunovska, Kalina; Schrader Echeverri, Elisa; Shajii, Aram; Peck, Hannah; Santangelo, Philip J; Dahlman, James E

Nanoparticle single-cell multiomic readouts reveal that cell heterogeneity influences lipid nanoparticle-mediated messenger RNA delivery

纳米颗粒单细胞多组学分析表明,细胞异质性会影响脂质纳米颗粒介导的信使RNA递送。

Curtis Dobrowolski # ,Kalina Paunovska # ,Elisa Schrader Echeverri ,David Loughrey ,Alejandro J Da Silva Sanchez ,Huanzhen Ni ,Marine Z C Hatit ,Melissa P Lokugamage ,Yanina Kuzminich ,Hannah E Peck ,Philip J Santangelo ,James E Dahlman

Species-dependent in vivo mRNA delivery and cellular responses to nanoparticles

物种依赖性体内 mRNA 传递和细胞对纳米粒子的反应

Marine Z C Hatit #, Melissa P Lokugamage #, Curtis N Dobrowolski #, Kalina Paunovska, Huanzhen Ni, Kun Zhao, Daryll Vanover, Jared Beyersdorf, Hannah E Peck, David Loughrey, Manaka Sato, Ana Cristian, Philip J Santangelo, James E Dahlman

Piperazine-derived lipid nanoparticles deliver mRNA to immune cells in vivo

哌嗪衍生的脂质纳米颗粒可将mRNA递送至体内免疫细胞。

Ni, Huanzhen; Hatit, Marine Z C; Zhao, Kun; Loughrey, David; Lokugamage, Melissa P; Peck, Hannah E; Cid, Ada Del; Muralidharan, Abinaya; Kim, YongTae; Santangelo, Philip J; Dahlman, James E

Therapeutic RNA Delivery for COVID and Other Diseases

用于治疗新冠肺炎和其他疾病的治疗性RNA递送

Dobrowolski, Curtis; Paunovska, Kalina; Hatit, Marine Z C; Lokugamage, Melissa P; Dahlman, James E