Correcting a patient-specific Rhodopsin mutation with adenine base editor in a mouse model
利用腺嘌呤碱基编辑器在小鼠模型中纠正患者特异性视紫红质突变
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.03.021
He, Xiaoxue; Yan, Tong; Song, Zongming; Xiang, Lue; Xiang, Jiayang; Yang, Yeqin; Ren, Kaiqun; Bu, Jicheng; Xu, Xilin; Li, Zhuo; Guo, Xiaowei; Lin, Bin; Zhou, Qinghua; Lin, Ge; Gu, Feng