日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Comparative Efficacy and Safety of Anakinra and Canakinumab in Patients With VEXAS Syndrome: An International Multicenter Study

阿那白滞素和卡那单抗治疗VEXAS综合征患者的疗效和安全性比较:一项国际多中心研究

Eviatar, Tali; Capelusnik, Dafne; Campochiaro, Corrado; Lacombe, Valentin; Jachiet, Vincent; Zisapel, Michael; Sagy, Iftach; Tayer-Shifman, Oshrat E; Ozeri, David; Kivity, Shaye; Tomelleri, Alessandro; Terrier, Benjamin; Peleg, Hagit; Comont, Thibault; Sacre, Karim; Woaye-Hune, Pascal; Arnaud, Laurent; Lazaro, Estibaliz; Grobost, Vincent; Lifermann, Francois; Samson, Maxime; Ardois, Samuel; Garnier, Alice; Maria, Alexandre; Cantagrel, Alain; Meyer, Aurore; Bouaziz, Jean-David; Heiblig, Mael; Dagna, Lorenzo; Diral, Elisa; Kosmider, Olivier; Elkayam, Ori; Hadjadj, Jérôme; Georgin-Lavialle, Sophie; Fain, Olivier; Mekinian, Arsene

American College of Rheumatology Guidance Statement for Diagnosis and Management of VEXAS Developed by the International VEXAS Working Group Expert Panel

美国风湿病学会关于VEXAS诊断和治疗的指导声明,由国际VEXAS工作组专家组制定

Mekinian, Arsene; Georgin-Lavialle, Sophie; Ferrada, Marcela A; Savic, Sinisa; Koster, Matthew J; Kosmider, Olivier; Comont, Thibault; Heiblig, Mael; Arostegui, Juan I; Bosco, Annmarie; Bourguiba, Rim; Calvo, Katherine R; Cargo, Catherine; Cattaneo, Chiara; Chasset, François; Coelho, Henrique; Campochiaro, Corrado; Crisafulli, Francesca; Ducharme-Benard, Stephanie; Faria, Raquel; Franceschini, Franco; Frassi, Micol; Groarke, Emma M; Gurnari, Carmelo; Hakobyan, Yervand; Jamilloux, Yvan; Jurcut, Ciprian; Kirino, Yohei; Kulasekararaj, Austin; Kunimoto, Hiroyoshi; Madigan, Lauren M; Mann, Heřman F; Marvisi, Chiara; Milchert, Marcin; Morais, Sara; Sockel, Katja; Muratore, Francesco; Nakajima, Hideaki; Patnaik, Mrinal M; Regadas, Luísa; Robin, Marie; Rutgers, Abraham; Salvarani, Carlo; Sammel, Anthony M; Seebach, Joerg; Sujobert, Pierre; Tomelleri, Alessandro; Urbanski, Geoffrey; Vandergheynst, Frédéric; Vieira, Romana; Viswanatha, David S; Więsik-Szewczyk, Ewa; Diral, Elisa; Terrier, Benjamin; Patel, Bhavisha A; Fenaux, Pierre; Grayson, Peter C; Beck, David B

PAXIS: A Randomized, Double-Blind, Placebo-Controlled, Dose-Finding Phase 2 Study (Part 1) Followed by an Open-Label Period (Part 2) to Assess the Efficacy and Safety of Pacritinib in Patients with VEXAS Syndrome

PAXIS:一项随机、双盲、安慰剂对照、剂量探索性 II 期研究(第一部分)及后续开放标签期(第二部分),旨在评估帕克替尼治疗 VEXAS 综合征患者的疗效和安全性

Beck, David B; Heiblig, Maël; Savic, Sinisa; Ferrada, Marcela A; Mekinian, Arsène; Chowdhury, Onima; Hammond, Danielle; Weeks, Lachelle D; Gurnari, Carmelo; Kirino, Yohei; Georgin-Lavialle, Sophie; Buckley, Sarah A; Garcha, Raman; Harder, Bryan G; Koster, Matthew J

A niche driven mechanism determines response and a mutation-independent therapeutic approach for myeloid malignancies

微环境驱动机制决定了髓系恶性肿瘤的治疗反应和非突变依赖性治疗方法。

Ioanna Mosialou ,Abdullah M Ali ,Rossella Labella ,Brygida Bisikirska ,Alvaro Cuesta-Dominguez ,Paraskevi Vgenopoulou ,Ismarc Reyes ,Sanjana M Rao ,Anqi Wang ,Na Luo ,Marta Galan-Diez ,Junfei Zhao ,Brian J Chernak ,Jan Philipp Bewersdorf ,Kazuya Fukasawa ,Jiayu Su ,Jason Higa ,Rachel A Adams ,Adam L Corper ,Sergey Pampou ,Catherine M Woods ,Xiaomin Fan ,Roshan P Shah ,Julie Feldstein ,Na Liu ,Cui Liang ,Maël Heiblig ,Steven Kornblau ,Guillermo Garcia-Manero ,Ellin Berman ,Joseph G Jurcic ,Raul Rabadan ,Azra Raza ,Stavroula Kousteni

Ziftomenib in Relapsed or Refractory NPM1-Mutated AML

Ziftomenib治疗复发或难治性NPM1突变型急性髓系白血病

Wang, Eunice S; Montesinos, Pau; Foran, James; Erba, Harry; Rodríguez-Arbolí, Eduardo; Fedorov, Kateryna; Heiblig, Maël; Heidel, Florian H; Altman, Jessica K; Baer, Maria R; Ades, Lionel; Pettit, Kristen; Peterlin, Pierre; Papayannidis, Cristina; Berthon, Céline; Walter, Roland B; Shah, Mithun V; Balasubramanian, Suresh; Khawandanah, Mohamad; Salamero Garcia, Olga; Bergeron, Julie; Madanat, Yazan F; Roboz, Gail J; Ulrickson, Matthew; Redner, Robert L; McCloskey, James; Pigneux, Arnaud; de la Fuente Burguera, Adolfo; Mitra, Amitava; Soifer, Harris S; Tabachri, Marilyn; Zhang, Zijing; Riches, Marcie; Corum, Daniel; Leoni, Mollie; Issa, Ghayas C; Fathi, Amir T

Menin inhibition with revumenib for NPM1-mutated relapsed or refractory acute myeloid leukemia: the AUGMENT-101 study

使用revumenib抑制Menin治疗NPM1突变复发或难治性急性髓系白血病:AUGMENT-101研究

Arellano, Martha L; Thirman, Michael J; DiPersio, John F; Heiblig, Maël; Stein, Eytan M; Schuh, Andre C; Žučenka, Andrius; de Botton, Stephane; Grove, Carolyn S; Mannis, Gabriel N; Papayannidis, Cristina; Perl, Alexander E; Issa, Ghayas C; Aldoss, Ibrahim; Bajel, Ashish; Dickens, David S; Kühn, Michael W M; Mantzaris, Ioannis; Raffoux, Emmanuel; Traer, Elie; Amitai, Irina; Döhner, Hartmut; Greco, Corinna; Kovacsovics, Tibor; McMahon, Christine M; Montesinos, Pau; Pigneux, Arnaud; Shami, Paul J; Stone, Richard M; Wolach, Ofir; Harpel, John G; Chudnovsky, Yakov; Yu, Li; Bagley, Rebecca G; Smith, Angela R; Blachly, James S

Inflammatory disorders in IDH-mutated myeloid neoplasms: Characteristics and response to IDH inhibitors

IDH突变型髓系肿瘤的炎症性疾病:特征及对IDH抑制剂的反应

Stammler, Romain; Chen, Peter; Debeaupuis, Orianne; Zhao, Lin-Pierre; Ruyer-Thompson, Mirabelle; Zakine, Eve; Rossignol, Julien; Goldwirt, Lauriane; Comont, Thibault; Heiblig, Maël; Adès, Lionel; Sebert, Marie; Allain, Jean-Sébastien; Campagne, Julien; Couturier, Marie-Anne; Cumin, Marina; Dalmas, Marie-Caroline; Denis, Guillaume; Devloo, Cécile; De Voeght, Adrien; Drevon, Louis; Duffau, Pierre; Georgin-Lavialle, Sophie; Gobert, Delphine; Kosmider, Olivier; Rieux-Laucat, Frédéric; Abisror, Noémie; Lazaro, Estibaliz; Lopez, Jean-Guillaume; Maria, Alexandre; Mauhin, Wladimir; Merindol, Julie; Merlot, Claire; Mirault, Tristan; Pascal, Laurent; Perrin, François; Raffoux, Emmanuel; Rahme, Ramy; Roos-Weil, Damien; Terrier, Benjamin; Thoreau, Benjamin; Fain, Olivier; Fenaux, Pierre; Hirsch, Pierre; Jachiet, Vincent; Hadjadj, Jérôme; Mékinian, Arsène

Efficacy of erythroid-stimulating agent and luspatercept in VEXAS syndrome: A multicenter retrospective study by the FRENVEX group

红细胞刺激剂和鲁斯帕西普治疗VEXAS综合征的疗效:FRENVEX研究组的一项多中心回顾性研究

Heiblig, Maël; Jachiet, Vincent; Hadjadj, Jérôme; Zhao, Lin Pierre; Comont, Thibault; Lobbes, Hervé; Lacombe, Valentin; Boutin, Anne Blandine; Galland, Joris; Terrier, Benjamin; Georgin-Lavialle, Sophie; Fenaux, Pierre; Mekinian, Arsène

Myeloid neoplasms after CD19-directed CAR T cells therapy in long-term B-cell lymphoma responders, a rising risk over time?

长期接受 CD19 靶向 CAR T 细胞疗法治疗的 B 细胞淋巴瘤患者发生髓系肿瘤的风险是否会随时间推移而增加?

Gazeau, Nicolas; Beauvais, David; Tilmont, Rémi; Srour, Micha; Ferrant, Emmanuelle; Safar, Violaine; Fouillet, Ludovic; Flandrin-Gresta, Pascale; Gower, Nicolas; Chauvet, Paul; Duployez, Nicolas; Podvin, Benjamin; Demaret, Julie; Huet, Sarah; Sujobert, Pierre; Ghesquières, Hervé; Damaj, Gandhi; Bachy, Emmanuel; Morschhauser, Franck; Yakoub-Agha, Ibrahim; Heiblig, Maël; Sesques, Pierre

Genetic and Phenotypic Correlates of Clinical Outcomes with Venetoclax in Acute Myeloid Leukemia: The GEN-PHEN-VEN Study

维奈托克治疗急性髓系白血病临床结局的遗传和表型相关性:GEN-PHEN-VEN 研究

Lachowiez, Curtis A; Heiblig, Mael; Aspas Requena, Gaspar; Tavernier-Tardy, Emmanuelle; Dai, Fangyan; Ashango, Amenech B; Peters, Daniel T; Fang, Jacob; Kaempf, Andy; Long, Nicola; Eide, Christopher A; Kurtz, Stephen E; Xie, Wei; Agarwal, Anupriya; Sahasrabudhe, Aishwarya; McMahon, Christine M; Amaya, Maria L; Meyers, Gabrielle; Gandhi, Arpita; Leonard, Jessica; Hayes-Lattin, Brandon; Maziarz, Richard T; Traer, Elie; Cook, Rachel J; Swords, Ronan; Braun, Theodore P; Saultz, Jennifer N; Eckel, Ashley M; Loken, Michael R; Zeidner, Joshua F; Tyner, Jeffrey W; Pollyea, Daniel A