Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa
配对缺口介导的 COL17A1 重构用于治疗交界性大疱性表皮松解症
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2022.04.020
Johannes Bischof, Oliver Patrick March, Bernadette Liemberger, Simone Alexandra Haas, Stefan Hainzl, Igor Petković, Victoria Leb-Reichl, Julia Illmer, Evgeniia Korotchenko, Alfred Klausegger, Anna Hoog, Heide-Marie Binder, Marta Garcia, Blanca Duarte, Dirk Strunk, Fernando Larcher, Julia Reichelt, C