日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report

脐带血移植为缺乏HLA匹配供体的慢性肉芽肿病患者提供了一种替代方案:PIDTC报告

Arnold, Danielle E; Leiding, Jennifer W; Logan, Brent; Marsh, Rebecca A; Griffith, Linda M; Grunebaum, Eyal; Murguía-Favela, Luis; Mallhi, Kanwaldeep; Chellapandian, Deepakbabu; Deal, Christin L; Lim, Stephanie Si; Prasad, Vinod; Heimall, Jennifer; Chandrakasan, Shanmuganathan; Chen, Karin; Yu, Lolie C; Seroogy, Christine M; Gillio, Alfred; Bednarski, Jeffrey J; Kapoor, Neena; Moore, Theodore B; Cuvelier, Geoffrey D E; Touzot, Fabien; Rayes, Ahmad; Ebens, Christen L; Schaefer, Edo; Bauchat, Andrea; Chopek, Ashley; Burroughs, Lauri; Cowan, Morton J; Dvorak, Christopher C; Haddad, Elie; Kohn, Donald B; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Torgerson, Troy; Malech, Harry L; Kang, Elizabeth M; Parikh, Suhag

Clinical spectrum of Wiskott-Aldrich syndrome carriers: Self-reported survey of 193 carriers

Wiskott-Aldrich综合征携带者的临床表现谱:193名携带者的自我报告调查

Chandrakasan, Shanmuganathan; Westbrook, Adrianna; Griffith, Linda M; Hagin, David; Iyengar, Sumathi; Mangurian, Christina; Scalchunes, Chris; Sullivan, Kathleen E; Zablocki, Akiva; Bakshi, Nitya; Sinha, Cynthia; Burroughs, Lauri M; Chan, Alice Y; Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Kohn, Donald B; Leiding, Jennifer W; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Marsh, Rebecca A; Torgerson, Troy; Cowan, Morton J; Ochs, Hans D; Parikh, Suhag

Unmanipulated bone marrow infusion without conditioning can rescue RECQL4 (-/-) severe combined immunodeficiency

未经处理的骨髓输注(无需预处理)可以挽救RECQL4(-/-)重症联合免疫缺陷患者。

Grier, Alexandra E; Bosticardo, Marita; Pala, Francesca; Delmonte, Ottavia M; Amini, Kayla; Anaya, Eduardo; Romberg, Neil; McClory, Susan E; Bunin, Nancy J; Abdalgani, Manar; Notarangelo, Luigi D; Heimall, Jennifer

Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study

造血干细胞移植治疗重症联合免疫缺陷(SCID)患者的神经发育结局:一项PIDTC研究

Brumm, Virdette L; Kidd, Sharon A; Logan, Brent R; Chunara, Farheen; Heimall, Jennifer; Griffith, Linda M; Kohn, Donald B; Sanchez, Lauren; Bednarski, Jeffrey J; Martinez, Caridad; Lugt, Mark Vander; Kapoor, Neena; Wright, Nicola; Spitzer, Barbara; Oved, Joseph H; Chandra, Sharat; Chellapandian, Deepak; Ebens, Christen L; Petrovic, Aleks; Rayes, Ahmad; Haines, Hilary L; Lust, Hannah; Schofield, Hannah-Lise Tirado; Christopher, Lauren; Harris, Lynnette L; Satter, Lisa Forbes; Burroughs, Lauri; Dvorak, Christopher C; Haddad, Elie; Leiding, Jennifer W; Marsh, Rebecca A; Notarangelo, Luigi D; Pai, Sung Yun; Pulsipher, Michael A; Puck, Jennifer M; Cowan, Morton J; Shah, Ami J

International clinical consensus on leukocyte adhesion deficiency-I: Modified Delphi analysis

关于白细胞黏附缺陷的国际临床共识-I:改良德尔菲分析

Heimall, Jennifer; González-Granado, Luis Ignacio; Booth, Claire; Ip, Winnie; Kuo, Caroline Y; Bakhtiar, Shahrzad; Ikincioğullari, Aydan; Ferrua, Francesca; Chitty-Lopez, Maria; Bailey, Miranda; Carter, Patrice; Matthews, Emily; Lee, Jennifer; Prockop, Susan; Gennery, Andrew R; Leiding, Jennifer W

Outcomes of Allogeneic Hematopoietic Stem Cell Transplant in Monogenic Inflammatory Bowel Disease

单基因炎症性肠病异基因造血干细胞移植的疗效

Baccarella, Alyssa; Patel, Trusha; Conrad, Maire A; Macchi, Marina; Boyer, Brooke; Pickering, Oliver; Borodyanskaya, Yelizaveta; Gaddipati, Shreya; Cohen, Maya; Cubero, Andrea; Dawany, Noor; Heimall, Jennifer; Bunin, Nancy; Sullivan, Kathleen E; Kelsen, Judith R

A survey of team culture and learning organization in the resuscitation of neonates with congenital anomalies: A single center experience

一项关于先天性异常新生儿复苏中团队文化和学习型组织的调查:单中心经验

Bostwick, Anna; Ades, Anne; Rodriguez-Paras, Carolina; Dombroski, Madeline; Lim, Charis; Paredes, Maria Ordoñez; Heimall, Lauren; Soorikian, Leane; Handley, Sara C; Herrick, Heidi M

120 Imaging and CSF biomarkers to optimize neurosurgical intervention for post-hemorrhagic hydrocephalus of prematurity

120 影像学和脑脊液生物标志物在优化早产儿出血后脑积水神经外科干预中的应用

Vigneron, Lara M; Duflot, Marc P; Robe, Pierre A; Warfield, Simon K; Verly, Jacques G; Flanders, Tracy; Hwang, Misun; Julian, Nickolas W; Sarris, Christina E; Flibotte, John J; DeMauro, Sara B; Munson, David A; Heimall, Lauren M; Collins, Yong C; Bamberski, Jena M; Sturak, Meghan A; Storm, Phillip B; Lang, Shih-Shan; Heuer, Gregory G