Selumetinib in adults with NF1 and inoperable plexiform neurofibroma: a phase 2 trial
Selumetinib治疗成人NF1合并不可手术的丛状神经纤维瘤:一项II期试验
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-024-03361-4
Gross, Andrea M; O'Sullivan Coyne, Geraldine; Dombi, Eva; Tibery, Cecilia; Herrick, William G; Martin, Staci; Angus, Steven P; Shern, Jack F; Rhodes, Steven D; Foster, Jared C; Rubinstein, Larry V; Baldwin, Andrea; Davis, Christopher; Dixon, Shelley A H; Fagan, Margaret; Ong, Mary Jane; Wolters, Pamela L; Tamula, Mary Anne; Reid, Olivia; Sankaran, Hari; Fang, Fang; Govindharajulu, Jeevan Prasaad; Browne, Alice T; Kaplan, Rosandra N; Heisey, Kara; On, Thomas J; Xuei, Xiaoling; Zhang, Xiyuan; Johnson, Barry C; Parchment, Ralph E; Clapp, D Wade; Srivastava, Apurva K; Doroshow, James H; Chen, Alice P; Widemann, Brigitte C