Increased phosphorylation of HexM improves lysosomal uptake and potential for managing GM2 gangliosidoses
HexM 磷酸化水平提高,可改善溶酶体摄取,提高治疗 GM2 神经节苷脂沉积症的潜力
期刊:BBA Advances
影响因子:
doi:10.1016/j.bbadva.2021.100032
Graeme Benzie, Kristen Bouma, Taylor Battellino, Steven Cooper, Rick Hemming, Wafa Kammouni, Lin Liu, Cuong Do, Mazdak Khajehpour, Helene Perreault, Stuart Kornfeld, Barbara Triggs-Raine, Brian L Mark