日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Inhaled DNAI1 mRNA therapy for treatment of primary ciliary dyskinesia.

吸入式 DNAI1 mRNA 疗法治疗原发性纤毛运动障碍

Hennig Mirko, Bhattacharjee Rumpa B, Agarwal Ishita, Alfaifi Ali, Casillas Jade E, Chavez Sofia, Ishimaru Daniella, Liston David, Mohapatra Sakya, Molla Touhidul, Pathare Suyog, Sidhu Maninder S, Wang Peng, Wang Zechen, Lombana T Noelle, Kharitonov Vladimir G, Couch Jessica A, Lockhart David J, Wustman Brandon A

Lipid nanoparticle-encapsulated Dnai1 mRNA rescues ciliary activity in primary ciliary dyskinesia mouse cell models

脂质纳米颗粒包裹的Dnai1 mRNA可挽救原发性纤毛运动障碍小鼠细胞模型中的纤毛活动。

Smith, Amanda J; Sears, Patrick R; Hennig, Mirko; Bhattacharjee, Rumpa B; Yin, Weining; Golliher, Hannah; Ishimaru, Daniella; Lombana, T Noelle; Lockhart, David J; Wustman, Brandon A; Ostrowski, Lawrence E

In vivo editing of lung stem cells for durable gene correction in mice

利用小鼠肺干细胞进行体内编辑以实现持久基因校正

Sun, Yehui; Chatterjee, Sumanta; Lian, Xizhen; Traylor, Zachary; Sattiraju, Sandhya R; Xiao, Yufen; Dilliard, Sean A; Sung, Yun-Chieh; Kim, Minjeong; Lee, Sang M; Moore, Stephen; Wang, Xu; Zhang, Di; Wu, Shiying; Basak, Pratima; Wang, Jialu; Liu, Jing; Mann, Rachel J; LePage, David F; Jiang, Weihong; Abid, Shadaan; Hennig, Mirko; Martinez, Anna; Wustman, Brandon A; Lockhart, David J; Jain, Raksha; Conlon, Ronald A; Drumm, Mitchell L; Hodges, Craig A; Siegwart, Daniel J

(1)H, (15)N and (13)C backbone resonance assignments of the N-terminal, tandem KH domains of human hnRNP E1

人hnRNP E1 N端串联KH结构域的(1)H、(15)N和(13)C骨架共振归属

Li, Yang; Hennig, Mirko

Development of inhibitors of heterotrimeric Gαi subunits

异源三聚体Gαi亚基抑制剂的开发

Appleton, Kathryn M; Bigham, Kevin J; Lindsey, Christopher C; Hazard, Starr; Lirjoni, Jonel; Parnham, Stuart; Hennig, Mirko; Peterson, Yuri K

Multivalent Amino Sugars to Recognize Different TAR RNA Conformations

多价氨基糖识别不同的TAR RNA构象

Kellish, Patrick C; Kumar, Sunil; Mack, Todd S; Spano, Meredith Newby; Hennig, Mirko; Arya, Dev P

The arginine-rich RNA-binding motif of HIV-1 Rev is intrinsically disordered and folds upon RRE binding

HIV-1 Rev蛋白中富含精氨酸的RNA结合基序本身是无序的,在与RRE结合后会发生折叠。

Casu, Fabio; Duggan, Brendan M; Hennig, Mirko

NMR assignments of the N-terminal domain of Nephila clavipes spidroin 1

对金蛛丝状蛋白1的N端结构域进行核磁共振归属

Parnham, Stuart; Gaines, William A; Duggan, Brendan M; Marcotte, William R Jr; Hennig, Mirko

A loop 2 cytidine-stem 1 minor groove interaction as a positive determinant for pseudoknot-stimulated -1 ribosomal frameshifting

环2胞嘧啶-茎1小沟相互作用作为假结刺激的-1核糖体移码的正向决定因素

Cornish, Peter V; Hennig, Mirko; Giedroc, David P