Liver-Targeted AAV-DJ-hCBS Therapy Achieves Long-Term Correction of Metabolic Imbalance in CBS-Deficient Mice
肝脏靶向AAV-DJ-hCBS疗法可长期纠正CBS缺陷小鼠的代谢失衡
期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms27073338
Joschko, Christian P; Wang, Chih-Chieh; van Buiten, Azuwerus; Goris, Maaike; Hoogstra-Berends, Femke; Wang, Joy; Bacurio, Jan Henric; Chen, Yinxing; Jia, Nannan; Deng, June; Hu, Shiliang; Nacht, Mariana; Chiocco, Matthew J; Henning, Robert H; Deelman, Leo E