Fancl-mutant mice reveal central role of monoubiquitination in Fanconi anemia and a model for therapeutic gene editing
Fancl突变小鼠揭示了单泛素化在范可尼贫血症中的核心作用,并为治疗性基因编辑提供了一种模型。
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2025017217
Liu, Lu; Glaser, Astrid; Isiaku, Abdulsalam I; Fairfax, Kirsten; Casolari, Debora A; Ristovski, Angelina; Murphy, Vincent; van Twest, Sylvie; Henrikus, Sarah S; Heraud-Farlow, Jacki; Granger, Elissah; Novakovic, Stevan; Monks O'Byrne, Sophie F; Tsui, Vanessa; Conyers, Rachel; Gonda, Thomas J; Crismani, Wayne; D'Andrea, Richard J; Heierhorst, Jörg; Deans, Andrew J