Selective C9orf72 G-Quadruplex-Binding Small Molecules Ameliorate Pathological Signatures of ALS/FTD Models
选择性C9orf72 G-四链体结合小分子可改善ALS/FTD模型的病理特征
期刊:Journal of Medicinal Chemistry
影响因子:6.8
doi:10.1021/acs.jmedchem.2c00654
Aifang Cheng,Changdong Liu,Wenkang Ye,Duli Huang,Weiyi She,Xin Liu,Chun Po Fung,Naining Xu,Monica Ching Suen,Wei Ye,Herman Ho Yung Sung,Ian Duncan Williams,Guang Zhu,Pei-Yuan Qian