In utero gene editing for monogenic lung disease
子宫内基因编辑治疗单基因肺病
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.aav8375
Alapati, Deepthi; Zacharias, William J; Hartman, Heather A; Rossidis, Avery C; Stratigis, John D; Ahn, Nicholas J; Coons, Barbara; Zhou, Su; Li, Hiaying; Singh, Kshitiz; Katzen, Jeremy; Tomer, Yaniv; Chadwick, Alexandra C; Musunuru, Kiran; Beers, Michael F; Morrisey, Edward E; Peranteau, William H