日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Unlocking the potential: m6A-RNA methylation in severe epidermolysis bullosa simplex.

释放潜能:严重单纯性大疱性表皮松解症中的 m6A-RNA 甲基化

Balacco Dario Leonardo, Hewitt Benjamin J, Bardhan Ajoy, Shriane Lisa M, Hunjan Manrup, Hickerson Robyn, Heagerty Adrian H M, Chapple Iain L

Therapeutic Prospects of Exon Skipping for Epidermolysis Bullosa

外显子跳跃治疗大疱性表皮松解症的治疗前景

Vermeer, Franciscus C; Bremer, Jeroen; Sietsma, Robert J; Sandilands, Aileen; Hickerson, Robyn P; Bolling, Marieke C; Pasmooij, Anna M G; Lemmink, Henny H; Swertz, Morris A; Knoers, Nine V A M; van der Velde, K Joeri; van den Akker, Peter C

Keratin 16 regulates innate immunity in response to epidermal barrier breach

角蛋白16在表皮屏障受损时调节先天免疫。

Lessard, Juliane C; Piña-Paz, Sylvia; Rotty, Jeremy D; Hickerson, Robyn P; Kaspar, Roger L; Balmain, Allan; Coulombe, Pierre A

Gene Silencing in Skin After Deposition of Self-Delivery siRNA With a Motorized Microneedle Array Device

利用电动微针阵列装置将自递送siRNA沉积到皮肤后实现基因沉默

Hickerson, Robyn P; Wey, Winston C; Rimm, David L; Speaker, Tycho; Suh, Susie; Flores, Manuel A; Gonzalez-Gonzalez, Emilio; Leake, Devin; Contag, Christopher H; Kaspar, Roger L

Designed guanidinium-rich amphipathic oligocarbonate molecular transporters complex, deliver and release siRNA in cells

设计的富含胍基的两亲性寡碳酸盐分子转运体复合物,可在细胞内递送和释放siRNA。

Geihe, Erika I; Cooley, Christina B; Simon, Jeff R; Kiesewetter, Matthew K; Edward, Justin A; Hickerson, Robyn P; Kaspar, Roger L; Hedrick, James L; Waymouth, Robert M; Wender, Paul A

Intravital fluorescence imaging of small interfering RNA-mediated gene repression in a dual reporter melanoma xenograft model

利用双报告基因黑色素瘤异种移植模型进行活体荧光成像,研究小干扰RNA介导的基因抑制。

Hickerson, Robyn P; Gonzalez-Gonzalez, Emilio; Vlassov, Alexander V; Li, Mu; Lara, Maria Fernanda; Contag, Christopher H; Kaspar, Roger L

Inhibition of CD44 gene expression in human skin models, using self-delivery short interfering RNA administered by dissolvable microneedle arrays

利用可溶解微针阵列递送的自递送短干扰RNA抑制人类皮肤模型中的CD44基因表达

Lara, Maria Fernanda; González-González, Emilio; Speaker, Tycho J; Hickerson, Robyn P; Leake, Devin; Milstone, Leonard M; Contag, Christopher H; Kaspar, Roger L

In vivo sustained release of siRNA from solid lipid nanoparticles

体内固体脂质纳米颗粒持续释放siRNA

Lobovkina, Tatsiana; Jacobson, Gunilla B; Gonzalez-Gonzalez, Emilio; Hickerson, Robyn P; Leake, Devin; Kaspar, Roger L; Contag, Christopher H; Zare, Richard N

First-in-human mutation-targeted siRNA phase Ib trial of an inherited skin disorder

首个针对遗传性皮肤病的人体突变靶向siRNA Ib期临床试验

Leachman, Sancy A; Hickerson, Robyn P; Schwartz, Mary E; Bullough, Emily E; Hutcherson, Stephen L; Boucher, Kenneth M; Hansen, C David; Eliason, Mark J; Srivatsa, G Susan; Kornbrust, Douglas J; Smith, Frances Jd; McLean, Wh Irwin; Milstone, Leonard M; Kaspar, Roger L

Silencing of reporter gene expression in skin using siRNAs and expression of plasmid DNA delivered by a soluble protrusion array device (PAD)

利用siRNA沉默皮肤中的报告基因表达,并通过可溶性突起阵列装置(PAD)递送质粒DNA表达

Gonzalez-Gonzalez, Emilio; Speaker, Tycho J; Hickerson, Robyn P; Spitler, Ryan; Flores, Manuel A; Leake, Devin; Contag, Christopher H; Kaspar, Roger L