Therapeutic Prospects of Exon Skipping for Epidermolysis Bullosa
外显子跳跃治疗大疱性表皮松解症的治疗前景
期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms222212222
Vermeer, Franciscus C; Bremer, Jeroen; Sietsma, Robert J; Sandilands, Aileen; Hickerson, Robyn P; Bolling, Marieke C; Pasmooij, Anna M G; Lemmink, Henny H; Swertz, Morris A; Knoers, Nine V A M; van der Velde, K Joeri; van den Akker, Peter C