A programmable dual-targeting di-valent siRNA scaffold supports potent multi-gene modulation in the central nervous system.
可编程双靶向二价siRNA支架支持中枢神经系统中有效的多基因调控
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doi:10.1101/2023.12.19.572404
Belgrad Jillian, Tang Qi, Hildebrand Sam, Summers Ashley, Sapp Ellen, Echeverria Dimas, O'Reilly Dan, Luu Eric, Bramato Brianna, Allen Sarah, Cooper David, Alterman Julia, Yamada Ken, Aronin Neil, DiFiglia Marian, Khvorova Anastasia