Development of a porcine model of phenylketonuria with a humanized R408W mutation for gene editing
开发具有人源化 R408W 突变的苯丙酮尿症猪模型以进行基因编辑
期刊:PLoS One
影响因子:2.9
doi:10.1371/journal.pone.0245831
Robert A Kaiser, Daniel F Carlson, Kari L Allen, Dennis A Webster, Caitlin J VanLith, Clara T Nicolas, Lori G Hillin, Yue Yu, Catherine W Kaiser, William R Wahoff, Raymond D Hickey, Adrienne L Watson, Shelley R Winn, Beat Thöny, Douglas R Kern, Cary O Harding, Joseph B Lillegard