日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Improved Iron Overload with Pegcetacoplan in Eculizumab-Experienced Patients with Paroxysmal Nocturnal Hemoglobinuria

在接受过依库珠单抗治疗的阵发性睡眠性血红蛋白尿患者中,使用培塞他考普兰可改善铁过载

Shammo, Jamile; Hillmen, Peter; Blandino, Peter; Abilash, Vijay; Kuter, David J

Efficacy and Safety Maintained up to 3 Years in Adults with Paroxysmal Nocturnal Hemoglobinuria Receiving Pegcetacoplan

在接受培塞他考普兰治疗的阵发性睡眠性血红蛋白尿成年患者中,疗效和安全性维持长达3年。

de Castro, Carlos; Kelly, Richard J; Griffin, Morag; Patriquin, Christopher J; Mulherin, Brian; Höchsmann, Britta; Selvaratnam, Veena; Wong, Raymond Siu Ming; Hillmen, Peter; Horneff, Regina; Uchendu, Uchendu O; Zhang, Yiwei; Surova, Elena; Szamosi, Johan; de Latour, Regis Peffault

The unfolded protein response influences therapy outcome and disease progression in chronic lymphocytic leukaemia.

未折叠蛋白反应影响慢性淋巴细胞白血病的治疗结果和疾病进展

Khan Umair Tahir, Clarke Kim, Eagle Gina, Oates Melanie, Hillmen Peter, Jayne Sandrine, Dyer Martin J S, Phipps Alex, Falciani Francesco, Jenkins Rosalind E, Pettitt Andrew R

Anchored Indirect Treatment Comparison Finds Comparable Effects of Pegcetacoplan and Iptacopan in Paroxysmal Nocturnal Haemoglobinuria

锚定间接治疗比较研究发现,在阵发性睡眠性血红蛋白尿症中,培塞他考普兰和伊普他考潘的疗效相当

de Latour, Regis Peffault; Kulasekararaj, Austin; Dingli, David; Wilson, Koo; Wojciechowski, Piotr; Hakimi, Zalmai; Nazir, Jameel; Czech, Barbara; Hillmen, Peter; Szer, Jeff

Six-year follow-up and subgroup analyses of a phase 2 trial of venetoclax for del(17p) chronic lymphocytic leukemia

一项针对del(17p)慢性淋巴细胞白血病的维奈托克II期临床试验的六年随访和亚组分析

Stilgenbauer, Stephan; Tausch, Eugen; Roberts, Andrew W; Davids, Matthew S; Eichhorst, Barbara; Hallek, Michael; Hillmen, Peter; Schneider, Christof; Schetelig, Johannes; Böttcher, Sebastian; Kater, Arnon P; Jiang, Yanwen; Boyer, Michelle; Popovic, Relja; Ghanim, Majd T; Moran, Michael; Sinai, Wendy J; Wang, Xifeng; Mukherjee, Nabanita; Chyla, Brenda; Wierda, William G; Seymour, John F

Navigating the Complement Pathway to Optimize PNH Treatment with Pegcetacoplan and Other Currently Approved Complement Inhibitors

利用补体通路优化Pegcetacoplan和其他已获批准的补体抑制剂治疗阵发性睡眠性血红蛋白尿症(PNH)

Hillmen, Peter; Horneff, Regina; Yeh, Michael; Kolev, Martin; Deschatelets, Pascal

Zanubrutinib Versus Ibrutinib in Relapsed/Refractory Chronic Lymphocytic Leukemia and Small Lymphocytic Lymphoma: Interim Analysis of a Randomized Phase III Trial

扎那布替尼与伊布替尼治疗复发/难治性慢性淋巴细胞白血病和小淋巴细胞淋巴瘤:一项随机III期试验的中期分析

Hillmen, Peter; Eichhorst, Barbara; Brown, Jennifer R; Lamanna, Nicole; O'Brien, Susan M; Tam, Constantine S; Qiu, Lugui; Kazmierczak, Maciej; Zhou, Keshu; Šimkovič, Martin; Mayer, Jiří; Gillespie-Twardy, Amanda; Shadman, Mazyar; Ferrajoli, Alessandra; Ganly, Peter S; Weinkove, Robert; Grosicki, Sebastian; Mital, Andrzej; Robak, Tadeusz; Österborg, Anders; Yimer, Habte A; Salmi, Tommi; Ji, Meng; Yecies, Jessica; Idoine, Adam; Wu, Kenneth; Huang, Jane; Jurczak, Wojciech

P786: THROMBOSIS AND MENINGOCOCCAL INFECTION RATES IN PEGCETACOPLAN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA IN THE CLINICAL TRIAL AND POST-MARKETING SETTINGS

P786:在临床试验和上市后研究中,接受聚乙二醇干扰素治疗的阵发性夜间血红蛋白尿患者的血栓形成率和脑膜炎球菌感染率

Kent, David G; Kaiser, Martin; Porter, John B; Eleftheriou, Perla; Drasar, Emma; Mullally, Ryan; Suri, Deepak; Le, Kim; Moon, James; Muth, Stephanie; St Pierre, Tim; Kelly, Richard; Nishimori, Hisakazu; Horneff, Regina; Hillmen, Peter; Savage, Jessica; Al-Adhami, Mohammed; Lallier, Stacie; Gerber, Gloria

Efficacy of coxsackievirus A21 against drug-resistant neoplastic B cells

柯萨奇病毒A21对耐药性肿瘤性B细胞的疗效

Holmes, Matthew; Scott, Gina B; Heaton, Samuel; Barr, Tyler; Askar, Basem; Müller, Louise M E; Jennings, Victoria A; Ralph, Christy; Burton, Cathy; Melcher, Alan; Hillmen, Peter; Parrish, Christopher; Errington-Mais, Fiona

Whole-genome sequencing of chronic lymphocytic leukemia identifies subgroups with distinct biological and clinical features

慢性淋巴细胞白血病的全基因组测序可识别出具有不同生物学和临床特征的亚群。

Robbe, Pauline; Ridout, Kate E; Vavoulis, Dimitrios V; Dréau, Helene; Kinnersley, Ben; Denny, Nicholas; Chubb, Daniel; Appleby, Niamh; Cutts, Anthony; Cornish, Alex J; Lopez-Pascua, Laura; Clifford, Ruth; Burns, Adam; Stamatopoulos, Basile; Cabes, Maite; Alsolami, Reem; Antoniou, Pavlos; Oates, Melanie; Cavalieri, Doriane; Gibson, Jane; Prabhu, Anika V; Schwessinger, Ron; Jennings, Daisy; James, Terena; Maheswari, Uma; Duran-Ferrer, Martí; Carninci, Piero; Knight, Samantha J L; Månsson, Robert; Hughes, Jim; Davies, James; Ross, Mark; Bentley, David; Strefford, Jonathan C; Devereux, Stephen; Pettitt, Andrew R; Hillmen, Peter; Caulfield, Mark J; Houlston, Richard S; Martín-Subero, José I; Schuh, Anna